Early view

Sep 28, 2023

Articles

Twist family BHLH transcription factor 1 is required for the maintenance of leukemia stem cell in MLL-AF9+ acute myeloid leukemia

Nan Wang, Jing Yin, Na You, Wenqi Zhu, Nini Guo, Xiaoyan Liu, Peiwen Zhang, Wanling Huang, Yueqiao Xie, Qian Ren, Xiaotong Ma

https://doi.org/10.3324/haematol.2023.282748

Ribosomal protein S3 mediates drug resistance of proteasome inhibitor: potential therapeutic application in multiple myeloma

Gege Chen, Xuejie Gao, Xinyan Jia, Yingcong Wang, Li Xu, Dandan Yu, Shuaikang Chang, Hui Deng, Ke Hu, Guanli Wang, Bo Li, Zhijian Xu, Yumeng Lu, Huaping Wang, Ting Zhang, Dongliang Song, Guang Yang, Xiaosong Wu, Huabin Zhu, Weiliang Zhu, Jumei Shi

https://doi.org/10.3324/haematol.2023.282789

Profiling the activity of the para-caspase MALT1 in B-cell acute lymphoblastic leukemia for potential targeted therapeutic application

Firas M. Safa, Terri Rasmussen, Lorena Fontan, Min Xia, Ari Melnick, Adrian Wiestner, Patricia Lobelle-Rich, Jan A. Burger, Yara Mouawad, Hana Safah, Erik K Flemington, Nakhle S. Saba

https://doi.org/10.3324/haematol.2023.283178

Polatuzumab vedotin plus bendamustine and rituximab or obinutuzumab in relapsed/refractory follicular lymphoma: a phase Ib/II study

Christopher R. Flowers, Matthew J. Matasar, Alex F. Herrera, Mark Hertzberg, Sarit Assouline, Judit Demeter, Andrew McMillan, Amitkumar Mehta, Stephen Opat, Marek Trnňný, Lisa Musick, Jamie Hirata, Annie Yang, Laurie H. Sehn

https://doi.org/10.3324/haematol.2023.283557

Regulatory T cells hamper the efficacy of T-cell engaging bispecific antibody therapy

Mika Casey, Carol Lee, Wing Yu Kwok, Soi Cheng Law, Dillon Corvino, Maher K Gandhi, Simon J Harrison, Kyohei Nakamura

https://doi.org/10.3324/haematol.2023.283758

HLA-C*04:09N is expressed at the cell surface and triggers peptide-specific T-cell activation

Carlotta Welters, Marthe-Lina Welters, Serena Stadler, Lars Bullinger, Julian Strobel, Holger Hackstein, Arunraj Dhamodaran, Thomas Blankenstein, Leo Hansmann

https://doi.org/10.3324/haematol.2023.283812

Letters to the Editor

Circulating tumor DNA and bone marrow minimal residual disease negativity confers superior outcome for multiple myeloma patients

Sridurga Mithraprabhu, John Reynolds, Hang Quach, Noemi Horvath, Ian Kerridge, Tiffany Khong, Brian GM Durie, Andrew Spencer

https://doi.org/10.3324/haematol.2023.283831

Engineering a humanized animal model of polycythemia vera with minimal JAK2V617Fmutant allelic burden

Tyler M. Parsons, Aishwarya Krishnan, Wangisa M.B. Dunuwille, Andrew L. Young, Jason Arand, Wentao Han, Grant A. Challen

https://doi.org/10.3324/haematol.2023.283858

Case Reports

An unusual case of thalassemia intermedia with inheritable complex repeats detected by single-molecule optical mapping

Qianqian Zhang, Peng Lin, Aiping Mao, Yongqiong Liu, Xuan Shang, Xiaofeng Wei, Yuezhen Li, Bin Lin, Xiangmin Xu

https://doi.org/10.3324/haematol.2023.282902

Concurrent peripheral T-cell lymphoma and T-cell lymphoblastic leukemia/lymphoma with identical STIL::TAL1 fusion events

Mahsa Khanlari, Wei Wang, Yen-Chun Liu, Lu Wang, Jeffrey E. Rubnitz, Stephanie Dixon, Brent A. Orr, Obianuju M. Anelo, Zhongshan Cheng, Vidya Balagopal, Jeffery M. Klco

https://doi.org/10.3324/haematol.2023.283585

Sep 21, 2023

Editorials
Article

Autonomous B-cell receptor signaling and genetic aberrations in chronic lymphocytic leukemia-phenotype monoclonal B lymphocytosis in siblings of patients with chronic lymphocytic leukemia (466 Online Views)

Edwin Quinten, Julieta H. Sepúlveda-Yáñez, Marvyn T. Koning, Janneke A. Eken, Dietmar Pfeifer, Valeri Nteleah, Ruben A.L. de Groen, Diego Alvarez Saravia, Jeroen Knijnenburg, Hedwig E. Stuivenberg-Bleijswijk, Milena Pantic, Andreas Agathangelidis, Andrea Keppler-Hafkemeyer, Cornelis A. M. van Bergen, Roberto Uribe-Paredes, Kostas Stamatopoulos, Joost S.P. Vermaat, Katja Zirlik, Marcelo A. Navarrete, Hassan Jumaa, Hendrik Veelken

https://doi.org/10.3324/haematol.2022.282542

Articles

Immune checkpoint molecule DNAM-1/CD112 axis is a novel target for NK-cell therapy in acute myeloid leukemia (137 Online Views)

Yuta Kaito, Emi Sugimoto, Fumi Nakamura, Yutaka Tsukune, Makoto Sasaki, Shunsuke Yui, Hiroki Yamaguchi, Susumu Goyama, Yasuhito Nannya, Kinuko Mitani, Hideto Tamura, Yoichi Imai

https://doi.org/10.3324/haematol.2023.282915

Dabrafenib and trametinib in Langerhans cell histiocytosis and other histiocytic disorders (147 Online Views)

Eily Cournoyer, Justin Ferrell, Susan Sharp, Anish Ray, Michael Jordan, Christopher Dandoy, Michael Grimley, Somak Roy, Robert Lorsbach, Arnold C. Merrow, Adam Nelson, Allison Bartlett, Jennifer Picarsic, Ashish Kumar

https://doi.org/10.3324/haematol.2023.283295

Idecabtagene vicleucel chimeric antigen receptor T-cell therapy for relapsed/refractory multiple myeloma with renal impairment (405 Online Views)

Surbhi Sidana, Lauren C. Peres, Hamza Hashmi, Hitomi Hosoya, Christopher Ferreri, Jack Khouri, Danai Dima, Shebli Atrash, Peter Voorhees, Gary Simmons, Douglas W. Sborov, Nilesh Kalariya, Vanna Hovanky, Sushma Bharadwaj, David Miklos, Charlotte Wagner, Mehmet H. Kocoglu, Gurbakhash Kaur, James A. Davis, Shonali Midha, Murali Janakiram, Ciara Freeman, Melissa Alsina, Frederick Locke, Rebecca Gonzalez, Yi Lin, Joseph McGuirk, Aimaz Afrough, Leyla Shune, Krina K. Patel, Doris K. Hansen

https://doi.org/10.3324/haematol.2023.283940

Letters to the Editor

Bone mineral density in adult patients with pyruvate kinase deficiency on long-term mitapivat treatment (67 Online Views)

Hanny Al-Samkari, Rachael F. Grace, Andreas Glenthøj, Oliver Andres, Wilma Barcellini, Frédéric Galacteros, Kevin H. M. Kuo, D. Mark Layton, Marta Morado, Vip Viprakasit, Feng Tai, Rolandas Urbstonaitis, Jaime Morales, Bryan McGee, Eduard J. van Beers

https://doi.org/10.3324/haematol.2023.282884

Outcome heterogeneity of TP53-mutated myeloid neoplasms and the role of allogeneic hematopoietic cell transplantation (86 Online Views)

Sergiu Pasca, Saurav D. Haldar, Alexander Ambinder, Jonathan A. Webster, Tania Jain, W. Brian Dalton, Gabrielle T. Prince, Gabriel Ghiaur, Amy E. DeZern, Ivana Gojo, B. Douglas Smith, Theodoros Karantanos, Cory Schulz, Kristin Stokvis, Mark J. Levis, Richard J. Jones, Lukasz P. Gondek

https://doi.org/10.3324/haematol.2023.283886

Sep 14, 2023

Review Articles

Articles

Treg-targeted IL-2/anti-IL-2 complex controls graft-versus-host disease and supports anti-tumor effect in allogeneic hematopoietic stem cell transplantation (219 Online Views)

Allan Thiolat, Caroline Pilon, Pamela Caudana, Audrey Moatti, Nhu Hanh To, Christine Sedlik, Mathieu Leclerc, Sébastien Maury, Eliane Piaggio, José L Cohen

https://doi.org/10.3324/haematol.2022.282653

Ultra-deep mutational landscape in chronic lymphocytic leukemia uncovers dynamics of resistance to targeted therapies (305 Online Views)

David W. Woolston, Nathan D. Lee, Mazyar Shadman, Elena Latorre-Esteves, Xin Ray Tee, Jeanne Fredrickson, Brendan F. Kohrn, Chaitra Ujjani, Ashley Eckel, Brian Till, Min Fang, Jerald Radich, Ivana Bozic, Rosa Ana Risques, Cecilia C.S. Yeung

https://doi.org/10.3324/haematol.2023.283372

Prognostic value of European Leukemia Net 2022 criteria and genomic clusters using machine learning in older adults with acute myeloid leukemia (160 Online Views)

Silvia Park, Tong Yoon Kim, Byung-Sik Cho, Daehun Kwag, Jong-Mi Lee, MyungShin Kim, Yonggoo Kim, Jamin Koo, Anjali Raman, Tae Kon Kim, Hee-Je Kim

https://doi.org/10.3324/haematol.2023.283606

Letters to the Editor

A phase II study of interrupted and continuous dose lenalidomide in relapsed/refractory Hodgkin lymphoma (395 Online Views)

Todd A. Fehniger, Marcus P. Watkins, Nkiruka Ezenwajiaku, Fei Wan, David D. Hurd, Amanda F. Cashen, Kristie A. Blum, Andre Goy, Timothy S. Fenske, Nina D. Wagner-Johnston, Kenneth Carson, Marilyn J. Siegel, David Russler-Germain, Stephanie E. Schneider, Neha Mehta-Shah, Brad Kahl, Nancy L. Bartlett

https://doi.org/10.3324/haematol.2022.282246

Amphiregulin as monitoring biomarker for life-threatening acute graft-versushost disease: secondary analysis of two prospective clinical trials (88 Online Views)

Shernan G. Holtan, Najla El Jurdi, Armin Rashidi, Brian C. Betts, Connor Demorest, John P Galvin, Margaret L. MacMillan, Daniel J. Weisdorf, Angela Panoskaltsis-Mortari, Michael A. Pratta

https://doi.org/10.3324/haematol.2023.283215

Oligosecretory Waldenstrom macroglobulinemia exhibits excellent treatment response and outcomes (235 Online Views)

Wenjie Xiong, Ying Yu, Chunyan Sun, Juan Du, Zhen Cai, Zanzan Wang, Xinxin Cao, Yuting Yan, Jiawen Chen, Yanshan Huang, Zhongxing Jiang, Huihan Wang, Ting Niu, Guangzhong Yang, Hua Xue, Bingzong Li, Honghui Huang, Zhenling Li, Qinhua Liu, Fei Li, Ou Bai, Min Mao, Rong Fu, Ling Wang, Chunrui Li, Xiaoxia Chu, Lihong Liu, Yujun Dong, Luqun Wang, Jun Luo, Yongqiang Wei, Rui Cui, Lugui Qiu, Jian Li, Shuhua Yi

https://doi.org/10.3324/haematol.2023.283402

Somatic variant profiling in chronic phase pediatric chronic myeloid leukemia (111 Online Views)

Yvonne Lisa Behrens, Laura Gaschler, Ronny Nienhold, Thea Reinkens, Elke Schirmer, Sabine Knöß, Renate Strasser, Stephanie Sembill, Zofia Wotschofsky, Meinolf Suttorp, Manuela Krumbholz, Brigitte Schlegelberger, Markus Metzler, Gudrun Göhring, Axel Karow

https://doi.org/10.3324/haematol.2023.283800

Case Reports

Sep 7, 2023

Editorials
Article

Genomic breakpoint specific monitoring of measurable residual disease in pediatric non-standard risk acute myeloid leukemia (331 Online Views)

Margarita Maurer-Granofszky, Stefan Kohrer, Susanna Fischer, Angela Schumich, Karin Nebral, Patrizia Larghero, Claus Meyer, Astrid Mecklenbrauker, Nora Muhlegger, Rolf Marschalek, Oskar A. Haas, Renate Panzer-Grumayer, Michael N. Dworzak

https://doi.org/10.3324/haematol.2022.282424

Editorials
Letter to the Editor

Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria (418 Online Views)

Austin G. Kulasekararaj, Anna-Elina Lehtinen, Cecily Forsyth, Shreyans Gandhi, Morag Griffin, Sixten Körper, Gabor Mikala, Petra Muus, Ulrik Overgaard, Christopher J. Patriquin, Humphrey Pullon, Yu-Min Shen, Ruth Spearing, Jeff Szer, Guillemette de la Borderie, Petra W. Duda, Ramin Farzaneh-Far, Sharan Ragunathan, Camil E. Sayegh, Douangsone D. Vadysirisack, Hubert Schrezenmeier

https://doi.org/10.3324/haematol.2022.281780

Editorials
Article

Ruxolitinib-based regimen in children with primary hemophagocytic lymphohistiocytosis (343 Online Views)

Jian Ge, Qing Zhang, Honghao Ma, Dong Wang, Yunze Zhao, Ting Zhu, Wenqian Wang, Chenxin Zhou, Ang Wei, Hongyun Lian, Maoquan Qin, Jun Yang, Zhigang Li, Tianyou Wang, Rui Zhang

https://doi.org/10.3324/haematol.2023.283478

Articles

Dynamic actin/septin network in megakaryocytes co-ordinates proplatelet elaboration (384 Online Views)

Isabelle C. Becker, Adrian R. Wilkie, Bret A. Unger, Anthony R. Sciaudone, Farheen Fatima, I-Ting Tsai, Ke Xu, Kellie R. Machlus, Joseph E. Italiano

https://doi.org/10.3324/haematol.2023.283369

Letters to the Editor

Prognostic value of minimal disseminated disease assessed using digital PCR for 3′ALK assays in pediatric anaplastic lymphoma kinase-positive anaplastic large cell lymphoma (97 Online Views)

Reiji Fukano, Yuka Iijima-Yamashita, Hideto Iwafuchi, Atsuko Nakazawa, Akiko M. Saito, Tetsuya Takimoto, Masahiro Sekimizu, Yutaka Suehiro, Takahiro Yamasaki, Shunji Hasegawa, Tetsuya Mori, Keizo Horibe

https://doi.org/10.3324/haematol.2023.282812

Frequent, high density expression of surface CD38 as a potential therapeutic target in adult T-lineage acute lymphoblastic leukemia (120 Online Views)

Sebastian Koslowski, Rainer Glauben, Stefan Habringer, Thomas Burmeister, Ulrich Keller, Monika Brüggemann, Nicola Gökbuget, Stefan Schwartz

https://doi.org/10.3324/haematol.2023.283814

Case Reports

Immune-mediated facial nerve paralysis in a myeloma patient post B-cell maturation antigen-targeted chimeric antigen receptor T cells (176 Online Views)

Yamini K. Kathari, Haroon Ahmad, Michael E. Kallen, Rima Koka, Destiny Omili, Thierry Iraguha, Jean Clement, Lily Pham, Mazhar Khalid, Xiaoxuan Fan, Etse Gebru, Patricia Lesho, Esther Park, Nishanthini Dishanthan, Jillian M. Baker, Kenneth A. Dietze, Kim G. Hankey, Ashraf Badros, Jean A. Yared, Saurabh Dahiya, Nancy M. Hardy, Hakan Kocoglu, Tim Luetkens, Aaron P. Rapoport, Djordje Atanackovic

https://doi.org/10.3324/haematol.2023.283296

Aug 31, 2023

Articles

Which is the best treatment strategy before autologous peripheral blood stem cell transplantation in POEMS syndrome? (141 Online Views)

Francesco Autore, Stefania Bramanti, Federica Lessi, Idanna Innocenti, Eugenio Galli, Serena Rocchi, Rossella Ribolla, Daniele Derudas, Stefania Oliva, Paola Stefanoni, Magda Marcatti, Angelo Schenone, Giorgio La Nasa, Claudia Crippa, Elena Zamagni, Marcello Riva, Rita Mazza, Daniele Mannina, Simona Sica, Andrea Bacigalupo, Luca Laurenti

https://doi.org/10.3324/haematol.2023.283719

Diffuse large B-cell lymphoma involving osseous sites: utility of response assessment by PET/CT and good long-term outcomes (393 Online Views)

Paola Ghione, Salma Ahsanuddin, Efrat Luttwak, Sabela Bobillo Varela, Reiko Nakajima, Laure Michaud, Kanika Gupta, Anastasia Navitski, David Straus, M. Lia Palomba, Alison Moskowitz, Ariela Noy, Paul Hamlin, Matthew Matasar, Anita Kumar, Lorenzo Falchi, Joachim Yahalom, Steven Horwitz, Andrew Zelenetz, Anas Younes, Gilles Salles, Heiko Schöder, Erel Joffe

https://doi.org/10.3324/haematol.2022.282643

Immunochemotherapy plus lenalidomide for high-risk mantle cell lymphoma with measurable residual disease evaluation (229 Online Views)

Zachary D. Epstein-Peterson, Esther Drill, Umut Aypar, Connie Lee Batlevi, Philip Caron, Ahmet Dogan, Pamela Drullinsky, John Gerecitano, Paul A. Hamlin, Caleb Ho, Allison Jacob, Ashlee Joseph, Leana Laraque, Matthew J. Matasar, Alison J. Moskowitz, Craig H. Moskowitz, Chelsea Mullins, Colette Owens, Gilles Salles, Heiko Schöder, David J. Straus, Anas Younes, Andrew D. Zelenetz, Anita Kumar

https://doi.org/10.3324/haematol.2023.282898

Lisocabtagene maraleucel for second-line relapsed or refractory large B-cell lymphoma: patient-reported outcomes from the PILOT study (424 Online Views)

Leo I. Gordon, Fei Fei Liu, Julia Braverman, Daanish Hoda, Nilanjan Ghosh, Mehdi Hamadani, Gerhard C. Hildebrandt, Lily Peng, Shien Guo, Ling Shi, Alison Sehgal

https://doi.org/10.3324/haematol.2023.283162

Loncastuximab tesirine in relapsed/refractory diffuse large B-cell lymphoma: long-term efficacy and safety from the phase 2 LOTIS-2 study (651 Online Views)

Paolo F. Caimi, Weiyun Z. Ai, Juan Pablo Alderuccio, Kirit M. Ardeshna, Mehdi Hamadani, Brian Hess, Brad S. Kahl, John Radford, Melhem Solh, Anastasios Stathis, Pier Luigi Zinzani, Ying Wang, Yajuan Qin, Luqiang Wang, Zhiying Cindy Xu, Carmelo Carlo-Stella

https://doi.org/10.3324/haematol.2023.283459

MYC protein is a high-risk factor in mantle cell lymphoma and identifies cases beyond morphology, proliferation and TP53/p53 – a Nordic Lymphoma Group study (304 Online Views)

Joana M. Rodrigues, Peter Hollander, Lina Schmidt, Eirinaios Gkika, Masoud Razmara, Darshan Kumar, Christian Geisler, Kirsten Grønbæk, Christian W. Eskelund, Riikka Räty, Arne Kolstad, Christer Sundström, Ingrid Glimelius, Anna Porwit, Mats Jerkeman, Sara Ek

https://doi.org/10.3324/haematol.2023.283352

Allogeneic hematopoietic stem cell transplantation in patients aged 60-79 years in Germany (1998-2018): a registry study (203 Online Views)

Jan Frederic Weller, Claudia Lengerke, Jürgen Finke, Johannes Schetelig, Uwe Platzbecker, Hermann Einsele, Thomas Schroeder, Christoph Faul, Matthias Stelljes, Peter Dreger, Igor W. Blau, Gerald Wulf, Johanna Tischer, Christoph Scheid, Ahmet Elmaagacli, Helga Neidlinger, Sarah Flossdorf, Martin Bornhäuser, Wolfgang Bethge, Katharina Fleischhauer, Nicolaus Kröger, Liesbeth C. de Wreede, Maximilian Christopeit

https://doi.org/10.3324/haematol.2023.283175

Quantification of cyclin D1 and D2 proteins in multiple myeloma identifies different expression patterns from those revealed by gene expression profiling (195 Online Views)

Ignacio J. Cardona-Benavides, Irena Misiewicz-Krzeminska, Elizabeta A. Rojas, Cristina De Ramón, Antonio Sanz-Solas, Isabel Isidro, Dalia Quwaider, Aida M. López-Guerrero, Myriam Cuadrado, María-José Calasanz, Laura Rosiñol, Joaquín Martínez-López, Jesús F. San Miguel, María-Victoria Mateos, Luis A. Corchete, Norma C. Gutiérrez

https://doi.org/10.3324/haematol.2023.283445

Tafasitamab for patients with relapsed or refractory diffuse large B-cell lymphoma: final 5-year efficacy and safety in the phase II L-MIND study (689 Online Views)

Johannes Duell, Pau Abrisqueta, Marc Andre, Gianluca Gaidano, Eva Gonzales-Barca, Wojciech Jurczak, Nagesh Kalakonda, Anna Marina Liberati, Kami J Maddocks, Tobias Menne, Zsolt Nagy, Olivier Tournilhac, Christian Kuffer, Abhishek Bakuli, Aasim Amin, Konstantin Gurbanov, Gilles Salles

https://doi.org/10.3324/haematol.2023.283480

ANCHOR: melflufen plus dexamethasone and daratumumab or bortezomib in relapsed/refractory multiple myeloma—final results of a phase I/IIa study (730 Online Views)

Enrique M. Ocio, Yvonne A. Efebera, Roman Hájek, Jan Straub, Vladimir Maisnar, Jean-Richard Eveillard, Lionel Karlin, María-Victoria Mateos, Albert Oriol, Vincent Ribrag, Paul G. Richardson, Stefan Norin, Jakob Obermüller, Nicolaas A. Bakker, Luděk Pour

https://doi.org/10.3324/haematol.2023.283490

Efficacy and safety of melflufen plus daratumumab and dexamethasone in relapsed/refractory multiple myeloma: results from the randomized, open-label, phase III LIGHTHOUSE study (1333 Online Views)

Luděk Pour, Monika Szarejko, Jelena Bila, Fredrik H. Schjesvold, Ivan Spicka, Vladimir Maisnar, Artur Jurczyszyn, Zhanet Grudeva-Popova, Roman Hájek, Ganna Usenko, Marcus Thuresson, Stefan Norin, Sara Jarefors, Nicolaas A. Bakker, Paul G. Richardson, Maria-Victoria Mateos

https://doi.org/10.3324/haematol.2023.283509

The changing spectrum of infection with BCMA and GPRC5D targeting bispecific antibody (bsAb) therapy in patients with relapsed refractory multiple myeloma (745 Online Views)

Lindsay Hammons, Aniko Szabo, Abhishek Janardan, Vineel Bhatlapenumarthi, Evanka Annyapu, Binod Dhakal, Samer Al Hadidi, Sabarinath Venniyil Radhakrishnan, Ravi Narra, Divaya Bhutani, Sharmilan Thanendrarajan, Siegfried Janz, Maurizio Zangari, Suzanne Lentzsch, Frits van Rhee, Juan Carlos Rico Crescencio, Anita D’Souza, Rajshekhar Chakraborty, Meera Mohan, Carolina Schinke

https://doi.org/10.3324/haematol.2023.283590

Prognostic relevance of clonal hematopoiesis in myeloid neoplastic transformation in patients with follicular lymphoma treated with radioimmunotherapy (165 Online Views)

Zhuoer Xie, Terra Lasho, Arushi Khurana, Alejandro Ferrer, Christy Finke, Abhishek A. Mangaonkar, Stephen Ansell, Jenna Fernandez, Mithun Vinod Shah, Aref Al-Kali, Naseema Gangat, Jithma Abeykoon, Thomas E. Witzig, Mrinal M. Patnaik

https://doi.org/10.3324/haematol.2023.283727

Letters to the Editor

Myeloid lineage switch in KMT2A-rearranged acute lymphoblastic leukemia treated with lymphoid lineage-directed therapies (234 Online Views)

Alex Bataller, Tareq Abuasab, David McCall, Wei Wang, Branko Cuglievan, Ghayas C. Issa, Elias Jabbour, Nicholas Short, Courtney D. DiNardo, Guilin Tang, Guillermo Garcia-Manero, Hagop M. Kantarjian, Koji Sasaki

https://doi.org/10.3324/haematol.2023.283705

Systemic and mucosal adaptive immunity to SARS-CoV-2 during the Omicron wave in patients with chronic lymphocytic leukemia (154 Online Views)

Hanna M. Ingelman-Sundberg, Lisa Blixt, David Wullimann, Jinghua Wu, Yu Gao, Katie Healy, Sandra Muschiol, Gordana Bogdanovic, Mikael Åberg, Christian Kjellander, Alba Grifoni, Alessandro Sette, Soo Aleman, Puran Chen, Ola Blennow, Lotta Hansson, Hans-Gustaf Ljunggren, Margaret Sällberg Chen, Marcus Buggert, Anders Österborg

https://doi.org/10.3324/haematol.2023.282894

Quantitative evaluation of the clinical severity of hemoglobin H disease in a cohort of 591 patients using a scoring system based on regression analysis (149 Online Views)

Yumeng Liu, Yuan Zhuang, Jianhong Chen, Zeyan Zhong, Jianpei Fang, Xinyu Li, Bin Xiao, Pingping Li, Bin Lin, Zhenzhong Tao, Yidan Liang, Peng Lin, Xingmin Wang, Mengyang Song, Hualei Luo, Lang Qin, Li Huang, Jufang Tan, Hailiang Li, Tianyu Zhong, Lian Yu, Zhixiang Liu, Deguo Tang, Yongzhong Zhao, Xinhua Zhang, Yuhua Ye, Xiangmin Xu

https://doi.org/10.3324/haematol.2023.283211

Survival disparities between children and adolescents and young adults for the major subtypes of non-Hodgkin lymphoma in the Netherlands: a large population-based study (146 Online Views)

Maya Schulpen, Auke Beishuizen, Martine E. D. Chamuleau, Avinash G. Dinmohamed, Friederike A. G. Meyer-Wentrup, H. Josef Vormoor, Lotte E. van der Wagen, Monique C. Minnema, Jan L. C. Loeffen, Henrike E. Karim-Kos

https://doi.org/10.3324/haematol.2023.283379

Thiostrepton induces cell death of acute myeloid leukemia blasts and the associated macrophage population (118 Online Views)

Isabel Weinhäuser, Diego A. Pereira-Martins, Jacobien R. Hilberink, Annet Brouwers-Vos, Eduardo M. Rego, Gerwin Huls, Jan Jacob Schuringa

https://doi.org/10.3324/haematol.2023.283621

Aug 24, 2023

Editorials
Article

BCL3-rearrangements in B-cell lymphoid neoplasms occur in two breakpoint clusters associated with different diseases (377 Online Views)

Anna Carbo-Meix, Francesca Guijarro, Luojun Wang, Marta Grau, Romina Royo, Gerard Frigola, Heribert Playa-Albinyana, Marco M. Buhler, Guillem Clot, Marti Duran-Ferrer, Junyan Lu, Isabel Granada, Maria-Joao Baptista, Jose-Tomas Navarro, Blanca Espinet, Anna Puiggros, Gustavo Tapia, Laura Bandiera, Gabriella De Canal, Emanuela Bonoldi, Fina Climent, Inmaculada Ribera-Cortada, Mariana Fernandez-Caballero, Esmeralda de la Banda, Janilson do Nascimento, Alberto Pineda, Dolors Vela, Maria Rozman, Marta Aymerich, Charlotte Syrykh, Pierre Brousset, Miguel Perera, Lucrecia Yanez, Jesus Xavier Ortin, Esperanza Tuset, Thorsten Zenz, James R. Cook, Steven H. Swerdlow, Jose I. Martin-Subero, Dolors Colomer, Estella Matutes, Silvia Bea, Dolors Costa, Ferran Nadeu, Elias Campo

https://doi.org/10.3324/haematol.2023.283209

Editorials
Article

Lymphocyte migration and retention properties affected by ibrutinib in chronic lymphocytic leukemia (623 Online Views)

Javier Rey-Barroso, Alice Munaretto, Nelly Rouquié, Aurélie Mougel, Malika Chassan, Sébastien Gadat, Océane Dewingle, Renaud Poincloux, Sarah Cadot, Loïc Ysebaert, Anne Quillet-Mary, Loïc Dupré

https://doi.org/10.3324/haematol.2022.282466

Review Articles

Clinical perspectives on the optimal use of lenalidomide plus bortezomib and dexamethasone for the treatment of newly diagnosed multiple myeloma (361 Online Views)

Paul G. Richardson, Brian G. Durie, Laura Rosiñol, Maria-Victoria Mateos, Angela Dispenzieri, Philippe Moreau, Shaji Kumar, Noopur Raje, Nikhil Munshi, Jacob P. Laubach, Peter O’Gorman, Elizabeth O’Donnell, Peter Voorhees, Thierry Facon, Joan Bladé, Sagar Lonial, Aurore Perrot, Kenneth C. Anderson

https://doi.org/10.3324/haematol.2022.282624

Articles

SUMOylation inhibitor TAK-981 (subasumstat) synergizes with 5-azacitidine in preclinical models of acute myeloid leukemia (699 Online Views)

Ludovic Gabellier, Marion De Toledo, Mehuli Chakraborty, Dana Akl, Rawan Hallal, Mays Aqrouq, Giovanni Buonocore, Clara Recasens-Zorzo, Guillaume Cartron, Abigaïl Delort, Marc Piechaczyk, Denis Tempé, Guillaume Bossis

https://doi.org/10.3324/haematol.2023.282704

Letters to the Editor

Identification of PSMB4 and PSMD4 as novel target genes correlated with 1q21 amplification in patients with smoldering myeloma and multiple myeloma (185 Online Views)

Jessica Burroughs Garcia, Paola Storti, Nicolas Thomas Iannozzi, Valentina Marchica, Luca Agnelli, Denise Toscani, Valentina Franceschi, Giannalisa Todaro, Gabriella Sammarelli, Laura Notarfranchi, Matteo Scita, Benedetta Dalla Palma, Vincenzo Raimondi, Oxana Lungu, Giancarlo Pruneri, Gaetano Donofrio, Nicola Giuliani

https://doi.org/10.3324/haematol.2023.283200

Aug 17, 2023

Editorials
Article

Current use of androgens in bone marrow failure disorders: a report from the Severe Aplastic Anemia Working Party of the European Society of Blood and Marrow Transplantation (979 Online Views)

Simona Pagliuca, Austin G. Kulasekararaj, Dirk-Jan Eikema, Brian Piepenbroek, Raheel Iftikhar, Tariq Mahmood Satti, Morag Griffin, Marica Laurino, Alphan Kupesiz, Yves Bertrand, Bruno Fattizzo, Ibrahim Yakoub-Agha, Mahmoud Aljurf, Paola Corti, Erika Massaccesi, Bruno Lioure, Marisa Calabuig, Matthias Klammer, Emel Unal, Depei Wu, Patrice Chevallier, Edouard Forcade, John A. Snowden, Hakan Ozdogu, Antonio Risitano, Régis Peffault de Latour

https://doi.org/10.3324/haematol.2023.282935

Editorials
Article

Aberrant MNX1 expression associated with t(7;12)(q36;p13) pediatric acute myeloid leukemia induces the disease through altering histone methylation (535 Online Views)

Ahmed Waraky, Anders Östlund, Tina Nilsson, Dieter Weichenhan, Pavlo Lutsik, Marion Bähr, Joschka Hey, Gürcan Tunali, Jenni Adamsson, Susanna Jacobsson, Mohammad Hamdy Abdelrazak Morsy, Susann Li, Linda Fogelstrand, Christoph Plass, Lars Palmqvist

https://doi.org/10.3324/haematol.2022.282255

Editorials
Letter to the Editor

Exclusion of persistent mutations in splicing factor genes and isocitrate dehydrogenase 2 improves the prognostic power of molecular measurable residual disease assessment in acute myeloid leukemia (283 Online Views)

Tracy Murphy, Jinfeng Zou, Andrea Arruda, Ting Ting Wang, Zhen Zhao, Yangqiao Zheng, Vikas Gupta, Dawn Maze, Caroline McNamara, Mark D. Minden, Aaron Schimmer, Hassan Sibai, Karen Yee, Jose-Mario Capo-Chichi, Tracy Stockley, Andre Schuh, Scott V. Bratman, Steven M. Chan

https://doi.org/10.3324/haematol.2023.283510

Review Articles

Articles

Isatuximab plus carfilzomib and dexamethasone in patients with early versus late relapsed multiple myeloma: IKEMA subgroup analysis (646 Online Views)

Thierry Facon, Philippe Moreau, Ross Baker, Chang-Ki Min, Xavier Leleu, Mohamad Mohty, Lionel Karlin, Nicole M. Armstrong, Christina Tekle, Sandrine Schwab, Marie-Laure Risse, Thomas Martin

https://doi.org/10.3324/haematol.2023.283073

Spontaneous remission and loss of monosomy 7: a window of opportunity for young children with SAMD9L syndrome (317 Online Views)

Miriam Erlacher, Felicia Andresen, Martina Sukova, Jan Stary, Barbara de Moerloose, Jutte van der Werff Ten Bosch, Michael Dworzak, Markus G. Seidel, Sophia Polychronopoulou, Rita Beier, Christian P. Kratz, Michaela Nathrath, Michael C. Frühwald, Gudrun Göhring, Anke K. Bergmann, Christina Mayerhofer, Dirk Lebrecht, Senthilkumar Ramamoorthy, Ayami Yoshimi, Brigitte Strahm, Marcin W. Wlodarski, Charlotte M. Niemeyer

https://doi.org/10.3324/haematol.2023.283591

Letters to the Editor

Red cell distribution width as a new prognostic biomarker in refractory chronic graft-versus-host disease (184 Online Views)

Eduard Schulz, Filip Pirsl, Noa G. Holtzman, David Beshensky, Edward W. Cowen, Sandra A. Mitchell, Seth M. Steinberg, Steven Z. Pavletic

https://doi.org/10.3324/haematol.2023.283646

Inflammation is predictive of outcome in Waldenström macroglobulinemia treated by Bruton tyrosine kinase inhibitors: a multicentric real-life study (259 Online Views)

Pierre-Edouard Debureaux, Nathalie Forgeard, Dikelele Elessa, Stéphanie Harel, Laurent Frenzel, Bruno Royer, Alexis Talbot, Sylvain Choquet, Frederic Davi, Florence Nguyen-Khac, Wendy Cuccuini, Morgane Cheminant, Clotilde Bravetti, Gregory Lazarian, Sophie Kaltenbach, Olivier Hermine, Damien Roos-Weil, Marion Espéli, Karl Balabanian, Bertrand Arnulf

https://doi.org/10.3324/haematol.2023.283141

SARS-CoV-2 vaccination in 361 non-transplanted patients with aplastic anemia and/or paroxysmal nocturnal hemoglobinuria (365 Online Views)

Morag Griffin, Dirk-Jan Eikema, Inge Verheggen, Alexander Kulagin, Jennifer M-L. Tjon, Bruno Fattizzo, Wendy Ingram, Uzma Zaidi, Lana Desnica, Sabrina Giammarco, Joanna Drozd-Sokolowska, Blanca Xicoy, Andrea Patriarca, Michael Loschi, Anna Szmigielska-Kaplon, Fabian Beier, Alessandro Cignetti, Beatrice Drexler, Eleni Gavriilaki, Francesco Lanza, Corentin Orvain, Antonio Maria Risitano, Rafael de la Camara, Régis Peffault de Latour

https://doi.org/10.3324/haematol.2023.283863

Spotlight Review

Aug 10, 2023

Articles

BCL3-rearrangements in B-cell lymphoid neoplasms occur in two breakpoint clusters associated with different diseases (377 Online Views)

Anna Carbo-Meix, Francesca Guijarro, Luojun Wang, Marta Grau, Romina Royo, Gerard Frigola, Heribert Playa-Albinyana, Marco M. Buhler, Guillem Clot, Marti Duran-Ferrer, Junyan Lu, Isabel Granada, Maria-Joao Baptista, Jose-Tomas Navarro, Blanca Espinet, Anna Puiggros, Gustavo Tapia, Laura Bandiera, Gabriella De Canal, Emanuela Bonoldi, Fina Climent, Inmaculada Ribera-Cortada, Mariana Fernandez-Caballero, Esmeralda de la Banda, Janilson do Nascimento, Alberto Pineda, Dolors Vela, Maria Rozman, Marta Aymerich, Charlotte Syrykh, Pierre Brousset, Miguel Perera, Lucrecia Yanez, Jesus Xavier Ortin, Esperanza Tuset, Thorsten Zenz, James R. Cook, Steven H. Swerdlow, Jose I. Martin-Subero, Dolors Colomer, Estella Matutes, Silvia Bea, Dolors Costa, Ferran Nadeu, Elias Campo

https://doi.org/10.3324/haematol.2023.283209

Feasibility and outcomes after dose reduction of immunochemotherapy in young adults with Burkitt lymphoma and leukemia: results of the BURKIMAB14 trial (222 Online Views)

Josep-Maria Ribera, Mireia Morgades, Olga Garcia-Calduch, Maialen Sirvent, Buenaventura Buendia, Marta Cervera, Hugo Luzardo, Jesus-Maria Hernandez-Rivas, Marta Sitges, Irene Garcia-Cadenas, Pau Abrisqueta, Pau Montesinos, Mariana Bastos-Oreiro, Maria-Paz Queipo de Llano, Pilar Bravo, Anna Torrent, Pilar Herrera, Antoni Garcia-Guinon, Ferran Vall-llovera, Josefina Serrano, Maria-Jose Terol, Juan-Miguel Bergua, Ana Garcia-Noblejas, Cristina Barrenetxea, Laura Llorente, Daniel Garcia-Belmonte, Eva Gimeno, Antonia Cladera, Santiago Mercadal, Juan-Manuel Sancho

https://doi.org/10.3324/haematol.2023.283342

Use, variability, and justification of eligibility criteria for phase II and III clinical trials in acute leukemia (320 Online Views)

Andrew Hantel, Marlise R. Luskin, Irum Khan, Elizabeth Warner, Anand A. Patel, Thomas P. Walsh, Daniel J. DeAngelo, Christopher S. Lathan, Gregory A. Abel

https://doi.org/10.3324/haematol.2023.283723

Aug 3, 2023

Editorials
Letter to the Editor

An accessible patient-derived xenograft model of low-risk myelodysplastic syndromes (239 Online Views)

Patric Teodorescu, Sergiu Pasca, InYoung Choi, Cynthia Shams, W. Brian Dalton, Lukasz P. Gondek, Amy E. DeZern, Gabriel Ghiaur

https://doi.org/10.3324/haematol.2023.282967

Editorials
Article

Effect of age and treatment on predictive value of measurable residual disease: implications for clinical management of adult patients with acute myeloid leukemia (331 Online Views)

Francesco Mannelli, Matteo Piccini, Sara Bencini, Giacomo Gianfaldoni, Benedetta Peruzzi, Roberto Caporale, Barbara Scappini, Laura Fasano, Elisa Quinti, Gaia Ciolli, Andrea Pasquini, Francesca Crupi, Sofia Pilerci, Fabiana Pancani, Leonardo Signori, Danilo Tarantino, Chiara Maccari, Vivian Paradiso, Francesco Annunziato, Paola Guglielmelli, Alessandro M. Vannucchi

https://doi.org/10.3324/haematol.2023.283196

Editorials

Articles

Phenotypic profiling of CD34+ cells by advanced flow cytometry improves diagnosis of juvenile myelomonocytic leukemia (249 Online Views)

Cristina Bugarin, Laura Antolini, Chiara Buracchi, Sergio Matarraz, Tiziana Angela Coliva, Vincent H. van der Velden, Tomasz Szczepanski, Elaine Sobral da Costa, Alita van der Sluijs, Michaela Novakova, Ester Mejstrikova, Stefan Nierkens, Fabiana Vieira de Mello, Paula Fernandez, Carmen Aanei, Łukasz Sędek, Luisa Strocchio, Riccardo Masetti, Laura Sainati, Jan Philippé, Maria Grazia Valsecchi, Franco Locatelli, Jacques J.M. van Dongen, Andrea Biondi, Alberto Orfao, Giuseppe Gaipa

https://doi.org/10.3324/haematol.2023.282805

Regulatory T-cell dysfunctions are associated with increase in tumor necrosis factor α in autoimmune hemolytic anemia and participate in Th17 polarization (361 Online Views)

Marion Ciudad, Sethi Ouandji, Baptiste Lamarthée, Claudie Cladière, Thibault Ghesquière, Martin Nivet, Marine Thébault, Romain Boidot, Agnès Soudry-Faure, Sandy Chevrier, Corentin Richard, Thibault Maillet, François Maurier, Hélène Greigert, Coraline Genet, André Ramon, Malika Trad, Valérie Predan, Philippe Saas, Maxime Samson, Bernard Bonnotte, Sylvain Audia

https://doi.org/10.3324/haematol.2023.282859

Hypomethylating agent decitabine sensitizes diffuse large B-cell lymphoma to venetoclax (304 Online Views)

Fen Zhu, Jennifer L. Crombie, Wei Ni, Nguyet-Minh Hoang, Swati Garg, Liam Hackett, Stephen J. F. Chong, Mary C. Collins, Lixin Rui, James Griffin, Matthew S. Davids

https://doi.org/10.3324/haematol.2023.283245

Quantification of measurable residual disease using duplex sequencing in adults with acute myeloid leukemia (295 Online Views)

Laura W. Dillon, Jake Higgins, Hassan Nasif, Megan Othus, Lan Beppu, Thomas H. Smith, Elizabeth Schmidt, Charles C. Valentine III, Jesse J. Salk, Brent L Wood, Harry P. Erba, Jerald P. Radich, Christopher S. Hourigan

https://doi.org/10.3324/haematol.2023.283520

Minor clone of del(17p) provides a reservoir for relapse in multiple myeloma (607 Online Views)

Jian Cui, Rui Lv, Tengteng Yu, Wenqiang Yan, Jingyu Xu, Huishou Fan, Lingna Li, Yuntong Liu, Chenxing Du, Shuhui Deng, Weiwei Sui, Yan Xu, Shuhua Yi, Dehui Zou, Lugui Qiu, Gang An

https://doi.org/10.3324/haematol.2023.283533

Letters to the Editor

Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria (418 Online Views)

Austin G. Kulasekararaj, Anna-Elina Lehtinen, Cecily Forsyth, Shreyans Gandhi, Morag Griffin, Sixten Körper, Gabor Mikala, Petra Muus, Ulrik Overgaard, Christopher J. Patriquin, Humphrey Pullon, Yu-Min Shen, Ruth Spearing, Jeff Szer, Guillemette de la Borderie, Petra W. Duda, Ramin Farzaneh-Far, Sharan Ragunathan, Camil E. Sayegh, Douangsone D. Vadysirisack, Hubert Schrezenmeier

https://doi.org/10.3324/haematol.2022.281780

Colchicine reduces inflammation in a humanized transgenic murine model of sickle cell disease (156 Online Views)

Raghda T. Fouda, Hemanth M. Cherukury, Stacy B. Kiven, Natalie R. Garcia, Donovan A. Argueta, Graham J. Velasco, Kalpna Gupta, John D. Roberts

https://doi.org/10.3324/haematol.2023.283377

Impaired T-cell response to mRNA vaccination heralds risk of COVID-19 in long-term allogeneic hematopoietic stem cell transplantation survivors (233 Online Views)

Sigrun Einarsdottir, Jesper Waldenström, Andreas Törnell, Johan Ringlander, Joakim B. Stenbäck, Sebastian Malmström, Kristoffer Hellstrand, Anna Martner, Martin Lagging

https://doi.org/10.3324/haematol.2023.283551

Molecular predictors of response and survival following IDH1/2 inhibitor monotherapy in acute myeloid leukemia (239 Online Views)

Naseema Gangat, Kristen McCullough, Maymona Abdelmagid, Omer Karrar, Marissa Powell, Aref Al-Kali, Hassan Alkhateeb, Kebede Begna, Abhishek Mangaonkar, Antoine Saliba, Mehrdad Hefazi Torghabeh, Mark Litzow, William Hogan, Mithun Shah, Mrinal Patnaik, Animesh Pardanani, Talha Badar, James Foran, Jeanne Palmer, Lisa Sproat, Cecilia Arana Yi, Ayalew Tefferi

https://doi.org/10.3324/haematol.2023.283732

Jul 27, 2023

Articles

DNAJC10 maintains survival and self-renewal of leukemia stem cells through PERK branch of the unfolded protein response (381 Online Views)

Minjing Li, Xingli Wu, Meiyang Chen, Shiyu Hao, Yue Yu, Xiang Li, Erdi Zhao, Ming Xu, Zhenhai Yu, Zhiqiang Wang, Ning Xu, Changzhu Jin, Yancun Yin

https://doi.org/10.3324/haematol.2023.282691

TTK/MPS1 inhibitor OSU-13 targets the mitotic checkpoint and is a potential therapeutic strategy for myeloma (273 Online Views)

Larissa Valle Guilhen Longo, Tiffany Hughes, Betina McNeil-Laidley, Francesca Cottini, Gerard Hilinski, Elizabeth Merritt, Don M. Benson

https://doi.org/10.3324/haematol.2023.282838

IgH 3’RR recombination uncovers a non-germinal center imprint and c-MYC-dependent IgH rearrangement in unmutated chronic lymphocytic leukemia (296 Online Views)

Israa Al Jamal, Milene Parquet, Kenza Guiyedi, Said Aoufouchi, Morwenna Le Guillou, David Rizzo, Justine Pollet, Marine Dupont, Melanie Boulin, Nathalie Faumont, Hend Boutouil, Fabrice Jardin, Philippe Ruminy, Chahrazed El Hamel, Justine Lerat, Samar Al Hamaoui, Nehman Makdissy, Jean Feuillard, Nathalie Gachard, Sophie Peron

https://doi.org/10.3324/haematol.2023.282897

PVT1 interacts with polycomb repressive complex 2 to suppress genomic regions with pro-apoptotic and tumour suppressor functions in multiple myeloma (363 Online Views)

Patrick Nylund, Berta Garrido-Zabala, Alba Atienza Párraga, Louella Vasquez, Paul Theodor Pyl, George Mickhael Harinck, Anqi Ma, Jian Jin, Fredrik Öberg, Antonia Kalushkova, Helena Jernberg Wiklund

https://doi.org/10.3324/haematol.2023.282965

Jul 20, 2023

Editorials
Letter to the Editor

Editorials
Article

Impact of viral hepatitis therapy in multiple myeloma and other monoclonal gammopathies linked to hepatitis B or C viruses (483 Online Views)

Alba Rodríguez-García, Nicolas Mennesson, Gema Hernandez-Ibarburu, María Luz Morales, Laurent Garderet, Lorine Bouchereau, Sophie Allain-Maillet, Eric Piver, Irene Marbán, David Rubio, Edith Bigot-Corbel, Joaquín Martínez-López, María Linares, Sylvie Hermouet

https://doi.org/10.3324/haematol.2023.283096

Editorials
Article

Outcomes after intensive chemotherapy for secondary and myeloidrelated changes acute myeloid leukemia patients aged 60 to 75 years old: a retrospective analysis from the PETHEMA registry (461 Online Views)

David Martínez-Cuadrón, Juan E. Megías-Vericat, Cristina Gil, Teresa Bernal, Mar Tormo, Pilar Martínez-Sánchez, Carlos Rodríguez-Medina, Josefina Serrano, Pilar Herrera, José A. Pérez Simón, María J. Sayas, Juan Bergua, Esperanza Lavilla-Rubira, Maria Luz Amigo, Celina Benavente, Jose L. López Lorenzo, Manuel M. Pérez-Encinas, María B. Vidriales, Mercedes Colorado, Beatriz de Rueda, Raimundo García-Boyero, Sandra Marini, Julio García-Suárez, María López-Pavía, Maria I. Gómez-Roncero, Víctor Noriega, Aurelio López, Jorge Labrador, Ana Cabello, Claudia Sossa, Lorenzo Algarra, Mariana Stevenazzi, Antonio Solana-Altabella, Blanca Boluda, Pau Montesinos

https://doi.org/10.3324/haematol.2022.282506

Editorials
Article

Adenosine signaling inhibits erythropoiesis and promotes myeloid differentiation (463 Online Views)

Mahmoud Mikdar, Marion Serra, Elia Colin, Romain Duval, Emilie-Fleur Gauthier, Yann Lamarre, Yves Colin, Caroline Le Van Kim, Thierry Peyrard, Bérengère Koehl, Slim Azouzi

https://doi.org/10.3324/haematol.2022.281823

Editorials
Article

Patient-reported treatment response in chronic graft-versus-host disease (401 Online Views)

Annie Im, Iskra Pusic, Lynn Onstad, Carrie L. Kitko, Betty K. Hamilton, Amin M. Alousi, Mary E. Flowers, Stefanie Sarantopoulos, Paul Carpenter, Jennifer White, Sally Arai, Najla El Jurdi, George Chen, Corey Cutler, Stephanie Lee, Joseph Pidala

https://doi.org/10.3324/haematol.2023.282734

Articles

S-adenosylmethionine biosynthesis is a targetable metabolic vulnerability in multiple myeloma (432 Online Views)

Yanmeng Wang, Catharina Muylaert, Arne Wyns, Philip Vlummens, Kim De Veirman, Karin Vanderkerken, Esther Zaal, Celia Berkers, Jérome Moreaux, Elke De Bruyne, Eline Menu

https://doi.org/10.3324/haematol.2023.282866

Fludarabine, cytarabine, and idarubicin with or without venetoclax in patients with relapsed/refractory acute myeloid leukemia (448 Online Views)

Rabia Shahswar, Gernot Beutel, Razif Gabdoulline, Adrian Schwarzer, Arnold Kloos, Christian Koenecke, Michael Stadler, Gudrun Gohring, Yvonne Lisa Behrens, Zhixiong Li, Louisa-Kristin Dallmann, Piroska Klement, Catherin Albert, Martin Wichmann, Yasmine Alwie, Axel Benner, Maral Saadati, Arnold Ganser, Felicitas Thol, Michael Heuser

https://doi.org/10.3324/haematol.2023.282912

Results from a phase I trial of pembrolizumab plus vorinostat in relapsed/refractory B-cell non-Hodgkin lymphoma (425 Online Views)

James Godfrey, Matthew Mei, Lu Chen, Joo Y. Song, Victoria Bedell, Elizabeth Budde, Saro Armenian, Sandrine Puverel, Liana Nikolaenko, Robert Chen, Shari Daniels, Neena Kennedy, Lacolle Peters, Steven T. Rosen, Stephen J. Forman, Leslie L. Popplewell, Larry W. Kwak, Alex F. Herrera

https://doi.org/10.3324/haematol.2023.283002

Changing trends in the risk factors for second primary malignancies after autologous stem cell transplantation for multiple myeloma before and after the introduction of proteasome inhibitors and immunomodulatory drugs (471 Online Views)

Hiroyuki Takamatsu, Tomohiro Matsuda, Shohei Mizuno, Tsutomu Takahashi, Shin-ichi Fuchida, Ichiro Hanamura, Keisuke Kataoka, Nobuhiro Tsukada, Morio Matsumoto, Akira Hangaishi, Noriko Doki, Naoyuki Uchida, Masashi Sawa, Yumiko Maruyama, Shingo Kurahashi, Koji Nagafuji, Yoriko Harazaki, Shinichi Kako, Shinsuke Iida, Tatsuo Ichinohe, Yoshinobu Kanda, Yoshiko Atsuta, Kazutaka Sunami; Multiple Myeloma Working Group in the Japanese Society for Transplantation and Cellular Therapy (Collaborative Group)

https://doi.org/10.3324/haematol.2023.283202

Ruxolitinib-based regimen in children with primary hemophagocytic lymphohistiocytosis (343 Online Views)

Jian Ge, Qing Zhang, Honghao Ma, Dong Wang, Yunze Zhao, Ting Zhu, Wenqian Wang, Chenxin Zhou, Ang Wei, Hongyun Lian, Maoquan Qin, Jun Yang, Zhigang Li, Tianyou Wang, Rui Zhang

https://doi.org/10.3324/haematol.2023.283478

Letters to the Editor

Final results and overall survival data from a phase II study of acalabrutinib monotherapy in patients with relapsed/refractory mantle cell lymphoma, including those with poor prognostic factors (923 Online Views)

Steven Le Gouill, Monika Długosz-Danecka, Simon Rule, Pier Luigi Zinzani, Andre Goy, Stephen D. Smith, Jeanette K. Doorduijn, Carlos Panizo, Bijal D. Shah, Andrew J. Davies, Richard Eek, Eric Jacobsen, Arnon P. Kater, Tadeusz Robak, Preetesh Jain, Roser Calvo, Lin Tao, Michael Wang

https://doi.org/10.3324/haematol.2022.282469

Optimizing transplantation procedures through identification of prognostic factors in second remission for children with acute myeloid leukemia with no prior history of transplant (238 Online Views)

Hisashi Ishida, Shin-ichi Tsujimoto, Daisuke Hasegawa, Hirotoshi Sakaguchi, Shohei Yamamoto, Masakatsu Yanagimachi, Katsuyoshi Koh, Akihiro Watanabe, Asahito Hama, Yuko Cho, Kenichiro Watanabe, Maiko Noguchi, Masanobu Takeuchi, Junko Takita, Kana Washio, Keisuke Kato, Takashi Koike, Yoshiko Hashii, Ken Tabuchi, Moeko Hino, Yoshiko Atsuta, Yasuhiro Okamoto

https://doi.org/10.3324/haematol.2023.283203

Vaccine utilization and overwhelming post-splenectomy infection risk factors in two asplenia cohorts (187 Online Views)

Matthew A. Soderstrom, Mechelle A. Miller, Qing Wang, William P. Hennrikus, Nora L. Watson, Ryan C. Costantino, Matthew J. Bradley, V. Koneti Rao, Nathan A. Boggs

https://doi.org/10.3324/haematol.2023.283419

Myeloid lineage switch following CD7-targeted chimeric antigen receptor T-cell therapy in relapsed/refractory T-cell acute lymphoblastic leukemia (389 Online Views)

Ibrahim Aldoss, Parastou Tizro, Davsheen Bedi, James K. Mangan, Mary C. Clark, David Spencer, Joo Y. Song, Sindhu Cherian, Raju Pillai, Young Kim, Nitin Mahajan, Ketevan Gendzekhadze, Mike James, Kenneth Jacobs, Jan Davidson-Moncada, Stephen J. Forman, Huan-You Wang, Michelle Afkhami

https://doi.org/10.3324/haematol.2023.283566

Case Reports

Immune-related adverse events with bispecific T-cell engager therapy targeting B-cell maturation antigen (247 Online Views)

Bénédicte Piron, Mathilde Bastien, Chloé Antier, Romain Dalla-Torre, Bastien Jamet, Thomas Gastinne, Viviane Dubruille, Philippe Moreau, Jérôme Martin, Antoine Bénichou, Cyrille Touzeau, Benoît Tessoulin

https://doi.org/10.3324/haematol.2023.282919

Spotlight Review

Jul 13, 2023

Editorials
Article

Early splenectomy in a large cohort of children with sickle cell anemia: risks and consequences (290 Online Views)

Aimen Mechraoui, Ghislaine Ithier, Justine Pages, Zinedine Haouari, Liza Ali, Arnaud Bonnard, Malika Benkerrou, Florence Missud, Berengère Koehl, Laurent Holvoet, Enora Le Roux, Valentine Brousse

https://doi.org/10.3324/haematol.2022.282556

Editorials
Article

Conditional survival and standardized mortality ratios of patients with severe aplastic anemia surviving at least one year after hematopoietic cell transplantation or immunosuppressive therapy (721 Online Views)

Ryotaro Nakamura, Bhavisha A. Patel, Soyoung Kim, F. Lennie Wong, Saro H. Armenian, Emma M. Groarke, Daniel A. Kessler, Kyle M. Hebert, Michael Heim, Mary Eapen, Neal S. Young

https://doi.org/10.3324/haematol.2023.282781

Editorials

Review Articles

Down syndrome and leukemia: from basic mechanisms to clinical advances (544 Online Views)

André Baruchel, Jean-Pierre Bourquin, John Crispino, Sergi Cuartero, Henrik Hasle, Johann Hitzler, Jan-Henning Klusmann, Shai Izraeli, Andrew A. Lane, Sébastien Malinge, Karen R. Rabin, Irene Roberts, Sandra Ryeom, Sarah K. Tasian, Elvin Wagenblast

https://doi.org/10.3324/haematol.2023.283225

Articles

Safety and efficacy of tenalisib in combination with romidepsin in patients with relapsed/refractory T-cell lymphoma: results from a phase I/II open-label multicenter study (359 Online Views)

Swaminathan P. Iyer, Auris Huen, Weiyun Z. Ai, Deepa Jagadeesh, Mary J. Lechowicz, Craig Okada, Tatyana A. Feldman, Paola Ghione, Juan P. Alderuccio, Rebecca Champion, Seo-Hyun Kim, Ann Mohrbacher, Kasi V. Routhu, Prajak Barde, Ajit M. Nair, Bradley M. Haverkos

https://doi.org/10.3324/haematol.2022.281875

Pro-inflammatory cells sustain leukemic clonal expansion in T-cell large granular lymphocyte leukemia (336 Online Views)

Cristina Vicenzetto, Vanessa Rebecca Gasparini, Gregorio Barila, Antonella Teramo, Giulia Calabretto, Elisa Rampazzo, Samuela Carraro, Valentina Trimarco, Livio Trentin, Monica Facco, Gianpietro Semenzato, Renato Zambello

https://doi.org/10.3324/haematol.2022.282306

IL6Myc mouse is an immunocompetent model for the development of aggressive multiple myeloma (316 Online Views)

Michael D. Pisano, Fumou Sun, Yan Cheng, Deepak Parashar, Vivian Zhou, Xuefang Jing, Ramakrishna Sompallae, Jenica Abrudan, Michael T. Zimmermann, Angela Mathison, Siegfried Janz, Miles A. Pufall

https://doi.org/10.3324/haematol.2022.282538

Autonomous B-cell receptor signaling and genetic aberrations in chronic lymphocytic leukemia-phenotype monoclonal B lymphocytosis in siblings of patients with chronic lymphocytic leukemia (466 Online Views)

Edwin Quinten, Julieta H. Sepúlveda-Yáñez, Marvyn T. Koning, Janneke A. Eken, Dietmar Pfeifer, Valeri Nteleah, Ruben A.L. de Groen, Diego Alvarez Saravia, Jeroen Knijnenburg, Hedwig E. Stuivenberg-Bleijswijk, Milena Pantic, Andreas Agathangelidis, Andrea Keppler-Hafkemeyer, Cornelis A. M. van Bergen, Roberto Uribe-Paredes, Kostas Stamatopoulos, Joost S.P. Vermaat, Katja Zirlik, Marcelo A. Navarrete, Hassan Jumaa, Hendrik Veelken

https://doi.org/10.3324/haematol.2022.282542

Cancer-specific mortality in multiple myeloma: a population-based retrospective cohort study (317 Online Views)

Arleigh McCurdy, Hsien Seow, Gregory P. Pond, Anastasia Gayowsky, Rajshekhar Chakraborty, Alissa Visram, Rayan Kaedbey, Anita D’Souza, Ghulam Rehman Mohyuddin, Tanya M. Wildes, Rafael Fonseca, Hira Mian

https://doi.org/10.3324/haematol.2023.282905

Actin-bundling protein L-plastin promotes megakaryocyte rigidity and dampens proplatelet formation (242 Online Views)

Li Guo, Shancy Jacob, Bhanu Kanth Manne, E. Motunrayo Kolawole, Siqi Guo, Xiang Wang, Darian Murray, Emilia A. Tugolukova, Irina Portier, Yasuhiro Kosaka, Cindy Barba, Matthew T. Rondina, Brian Evavold, Celeste Morley, Seema Bhatlekar, Paul F. Bray

https://doi.org/10.3324/haematol.2023.283016

Disease associations with monoclonal gammopathy of undetermined significance can only be evaluated using screened cohorts: results from the population-based iStopMM study (417 Online Views)

Aðalbjörg Ýr Sigurbergsdóttir, Sæmundur Rögnvaldsson, Sigrún Thorsteinsdóttir, Ingigerður Sverrisdóttir, Guðrún Ásta Sigurðardóttir, Brynjar Viðarsson, Páll Torfi Önundarson, Bjarni A. Agnarsson, Margrét Sigurðardóttir, Ingunn Þorsteinsdóttir, Ísleifur Ólafsson, Ásdís Rósa Þórðardóttir, Gauti Kjartan Gíslason, Andri Ólafsson, Malin Hultcrantz, Brian G. M. Durie, Stephen Harding, Ola Landgren, Thorvarður Jón Löve, Sigurður Yngvi Kristinsson

https://doi.org/10.3324/haematol.2023.283191

Elotuzumab plus pomalidomide and dexamethasone in relapsed/refractory multiple myeloma: a multicenter, retrospective real-world experience with 200 cases outside of controlled clinical trials (571 Online Views)

Massimo Gentile, Ernesto Vigna, Salvatore Palmieri, Monica Galli, Daniele Derudas, Roberto Mina, Roberta Della Pepa, Renato Zambello, Enrica Antonia Martino, Antonella Bruzzese, Silvia Mangiacavalli, Elena Zamagni, Catello Califano, Maurizio Musso, Concetta Conticello, Claudio Cerchione, Giuseppe Mele, Nicola Di Renzo, Massimo Offidani, Giuseppe Tarantini, Gloria Margiotta Casaluci, Angela Rago, Roberto Ria, Giuseppina Uccello, Gregorio Barilà, Gaetano Palumbo, Alessandra Pompa, Donatella Vincelli, Marino Brunori, Fabrizio Accardi, Valeria Amico, Angela Amendola, Raffaele Fontana, Velia Bongarzoni, Bernardo Rossini, Emilia Cotzia, Alessandro Gozzetti, Rita Rizzi, Nicola Sgherza, Eleonora Ferretti, Giuseppe Bertuglia, Davide Nappi, Maria Teresa Petrucci, Francesco Di Raimondo, Antonino Neri, Fortunato Morabito, Pellegrino Musto

https://doi.org/10.3324/haematol.2023.283251

DIS3 depletion in multiple myeloma causes extensive perturbation in cell cycle progression and centrosome amplification (404 Online Views)

Vanessa K. Favasuli, Domenica Ronchetti, Ilaria Silvestris, Noemi Puccio, Giuseppina Fabbiano, Valentina Traini, Katia Todoerti, Silvia Erratico, Alessia Ciarrocchi, Valentina Fragliasso, Domenica Giannandrea, Francesca Tumiatti, Raffaella Chiaramonte, Yvan Torrente, Palma Finelli, Eugenio Morelli, Nikhil C. Munshi, Niccolò Bolli, Antonino Neri, Elisa Taìana

https://doi.org/10.3324/haematol.2023.283274

Metabolic signatures of cardiorenal dysfunction in plasma from sickle cell patients as a function of therapeutic transfusion and hydroxyurea treatment (258 Online Views)

Angelo D’Alessandro, S. Mehdi Nouraie, Yingze Zhang, Francesca Cendali, Fabia Gamboni, Julie A. Reisz, Xu Zhang, Kyle W. Bartsch, Matthew D. Galbraith, Joaquin M. Espinosa, Victor R. Gordeuk, Mark T. Gladwin

https://doi.org/10.3324/haematol.2023.283288

Daratumumab in first-line treatment of patients with light chain amyloidosis and Mayo stage IIIb improves treatment response and overall survival (463 Online Views)

Sara Oubari, Ute Hegenbart, Renate Schoder, Maximilian Steinhardt, Maria Papathanasiou, Tienush Rassaf, Andreas Thimm, Tim Hagenacker, Eyad Naser, Ulrich Duhrsen, Hans C. Reinhardt, Martin Kortum, Hermine Agis, Stefan Schonland, Alexander Carpinteiro

https://doi.org/10.3324/haematol.2023.283325

Letters to the Editor

Cross-intolerance with bosutinib after prior tyrosine kinase inhibitors for Philadelphia chromosome-positive leukemia: long-term analysis of a phase I/II study (453 Online Views)

Jorge E. Cortes, Jeff H. Lipton, Vamsi Kota, Fausto Castagnetti, Sarit Assouline, Tim H. Brümmendorf, Eric Leip, Andrea Viqueira, Carlo Gambacorti-Passerini

https://doi.org/10.3324/haematol.2022.281944

Modified carfilzomib dosing is associated with improved treatment responses and longer time on treatment in patients with multiple myeloma (320 Online Views)

Abdullah M. Khan, Kiatlyn Dvorak, Qiuhong Zhao, Naresh Bumma, Francesca Cottini, Srinivas Devarakonda, Elvira Umyarova, Nidhi Sharma, Don Benson, Ashley Rosko

https://doi.org/10.3324/haematol.2022.282521

Co-stimulatory and immune checkpoint molecules are important in the tumor microenvironment of Hodgkin-like adult T-cell leukemia/lymphoma (200 Online Views)

Mai Takeuchi, Hiroaki Miyoshi, Yuichiro Semba, Kyohei Yamada, Kazutaka Nakashima, Kensaku Sato, Takuya Furuta, Mayuko Moritsubo, Yusuke Ogura, Ken Tanaka, Teppei Imamoto, Fumiko Arakawa, Kei Kohno, Koichi Ohshima

https://doi.org/10.3324/haematol.2023.283163

Higher cyclophosphamide dose grants optimal stem-cell collection after daratumumab-based induction in multiple myeloma (470 Online Views)

Carmine Liberatore, Tommaso Perini, Cecilia Passeri, Valeria Ferla, Francesca Fioritoni, Virginia Girlando, Ornella Iuliani, Alessia Orsini, Guido Montanaro, Francesca Farina, Alessandro Di Nicola, Rosamaria Nitti, Stefano Pulini, Sara Mastaglio, Stella Santarone, Milena Coppola, Sarah Marktel, Patrizia Accorsi, Fabio Ciceri, Magda Marcatti, Mauro Di Ianni

https://doi.org/10.3324/haematol.2023.283452

Jul 6, 2023

Articles

Genomic analysis of venous thrombosis in children with acute lymphoblastic leukemia from diverse ancestries (303 Online Views)

Yan Zheng, Wenjian Yang, Jeremie Estepp, Deqing Pei, Cheng Cheng, Clifford M. Takemoto, Hiroto Inaba, Sima Jeha, Ching-Hon Pui, Mary V. Relling, Seth E. Karol

https://doi.org/10.3324/haematol.2022.281582

Haploidentical donor hematopoietic cell transplantation for myelodysplastic/myeloproliferative overlap neoplasms: results from a North American collaboration (582 Online Views)

Tania Jain, Hua-Ling Tsai, Hany Elmariah, Pankit Vachhani, Theodoros Karantanos, Sarah A Wall, Lukasz P. Gondek, Asad Bashey, Alla Keyzner, Roni Tamari, Michael R. Grunwald, Sameem Abedin, Kalyan VG Nadiminti, Madiha Iqbal, Aaron T Gerds, Auro Viswabandya, Shannon R McCurdy, Monzr M. Al Malki, Ravi Varadhan, Haris Ali, Vikas Gupta, Richard J. Jones, Salman Otoukesh

https://doi.org/10.3324/haematol.2023.283426

Letters to the Editor

An accessible patient-derived xenograft model of low-risk myelodysplastic syndromes (239 Online Views)

Patric Teodorescu, Sergiu Pasca, InYoung Choi, Cynthia Shams, W. Brian Dalton, Lukasz P. Gondek, Amy E. DeZern, Gabriel Ghiaur

https://doi.org/10.3324/haematol.2023.282967

Jun 29, 2023

Editorials
Article

B-cell receptor reactivity against Rothia mucilaginosa in nodular lymphocyte-predominant Hodgkin lymphoma (538 Online Views)

Lorenz Thurner, Natalie Fadle, Evi Regitz, Sophie Roth, Onur Cetin, Igor Age Kos, Simon Mauro Hess, Julia Bein, Rainer Maria Bohle, Martine Vornanen, Christer Sundström, Laurence de Leval, Enrico Tiacci, Peter Borchmann, Andreas Engert, Viola Poeschel, Gerhard Held, Eva C. Schwarz, Frank Neumann, Klaus-Dieter Preuss, Markus Hoth, Ralf Küppers, Karola Lehman, Martin-Leo Hansmann, Sören L. Becker, Moritz Bewarder, Sylvia Hartmann

https://doi.org/10.3324/haematol.2023.282698

Articles

Lymphocyte migration and retention properties affected by ibrutinib in chronic lymphocytic leukemia (623 Online Views)

Javier Rey-Barroso, Alice Munaretto, Nelly Rouquié, Aurélie Mougel, Malika Chassan, Sébastien Gadat, Océane Dewingle, Renaud Poincloux, Sarah Cadot, Loïc Ysebaert, Anne Quillet-Mary, Loïc Dupré

https://doi.org/10.3324/haematol.2022.282466

Amyloidogenic light chains impair plasma cell survival (306 Online Views)

Marjorie Pick, Eyal Lebel, Sharona Elgavish, Hadar Benyamini, Yuval Nevo, Rachel Hertz, Jacob Bar-Tana, Paola Rognoni, Giampaolo Merlini, Moshe E. Gatt

https://doi.org/10.3324/haematol.2022.282484

Long non-coding RNA mitophagy and ALK anaplastic lymphoma associated transcript: a novel regulator of mitophagy in T cell lymphoma (424 Online Views)

Valentina Mularoni, Benedetta Donati, Annalisa Tameni, Veronica Manicardi, Francesca Reggiani, Elisabetta Sauta, Magda Zanelli, Marco Tigano, Emanuele Vitale, Federica Torricelli, Stefano Ascani, Giovanni Martino, Giorgio Inghirami, Francesca Sanguedolce, Alessia Ruffini, Alberto Bavieri, Stefano Luminari, Marco Pizzi, Angelo Paolo Dei Tos, Cinzia Fesce, Antonino Neri, Alessia Ciarrocchi, Valentina Fragliasso

https://doi.org/10.3324/haematol.2022.282552

Clonal hematopoiesis with DNMT3A and PPM1D mutations impairs regeneration in autologous stem cell transplant recipients (737 Online Views)

Patrick Stelmach, Sarah Richter, Sandra Sauer, Margarete A. Fabre, Muxin Gu, Christian Rohde, Maike Janssen, Nora Liebers, Rumyana Proynova, Niels Weinhold, Marc S. Raab, Hartmut Goldschmidt, Birgit Besenbeck, Petra Pavel, Sascha Laier, Andreas Trumpp, Sascha Dietrich, George S. Vassiliou, Carsten Müller-Tidow

https://doi.org/10.3324/haematol.2023.282992

Letters to the Editor

ETV6 fusions from insertions of exons 3-5 in pediatric hematologic malignancies (223 Online Views)

Sarah B. Mueller, Yana Pikman, Sarah K. Tasian, Lewis B. Silverman, Marian H. Harris, Harrison K. Tsai

https://doi.org/10.3324/haematol.2022.282498

CD47 expression in acute myeloid leukemia varies according to genotype (707 Online Views)

Andrea Marra, Ayse U Akarca, Giovanni Martino, Alan Ramsay, Stefano Ascani, Vincenzo Maria Perriello, Jenny O’Nions, Andrew J Wilson, Rajeev Gupta, Anna Childerhouse, Ian Proctor, Manuel Rodriguez-Justo, Sabine Pomplun, Maria Paola Martelli, Cristina Lo Celso, Brunangelo Falini, Teresa Marafioti

https://doi.org/10.3324/haematol.2023.283154

Jun 22, 2023

Editorials
Letter to the Editor

Measurable residual disease-guided therapy in intermediate-risk acute myeloid leukemia patients is a valuable strategy in reducing allogeneic transplantation without negatively affecting survival (569 Online Views)

Jesse M. Tettero, Lok Lam Ngai, Costa Bachas, Dimitri A. Breems, Thomas Fischer, Bjorn T. Gjertsen, Patrycja Gradowska, Laimonas Griskevicius, Jeroen J.W.M. Janssen, Gunnar Juliusson, Johan Maertens, Markus G. Manz, Thomas Pabst, Jakob Passweg, Kimmo Porkka, Peter J.M. Valk, Bob Löwenberg, Gert J. Ossenkoppele, Jacqueline Cloos

https://doi.org/10.3324/haematol.2022.282639

Review Articles

Articles

Genomic breakpoint specific monitoring of measurable residual disease in pediatric non-standard risk acute myeloid leukemia (331 Online Views)

Margarita Maurer-Granofszky, Stefan Kohrer, Susanna Fischer, Angela Schumich, Karin Nebral, Patrizia Larghero, Claus Meyer, Astrid Mecklenbrauker, Nora Muhlegger, Rolf Marschalek, Oskar A. Haas, Renate Panzer-Grumayer, Michael N. Dworzak

https://doi.org/10.3324/haematol.2022.282424

Interleukin-27 potentiates CD8+ T-cell-mediated anti-tumor immunity in chronic lymphocytic leukemia (411 Online Views)

Giulia Pagano, Iria Fernandez Botana, Marina Wierz, Philipp M. Roessner, Nikolaos Ioannou, Xiangda Zhou, Gheed Al-Hity, Coralie Borne, Ernesto Gargiulo, Susanne Gonder, Bin Qu, Basile Stamatopoulos, Alan G. Ramsay, Martina Seiffert, Anne Largeot, Etienne Moussay, Jerome Paggetti

https://doi.org/10.3324/haematol.2022.282474

Inhibition of GPIb-α-mediated apoptosis signaling enables cold storage of platelets (306 Online Views)

Irene Marini, Lisann Pelzl, Yoko Tamamushi, Chiara-Tanita Maettler, Andreas Witzemann, Karina Althaus, Stefanie Nowak-Harnau, Erhard Seifried, Tamam Bakchoul

https://doi.org/10.3324/haematol.2022.282572

Predictors of SARS-CoV-2 Omicron breakthrough infection after receipt of AZD7442 (tixagevimab-cilgavimab) for pre-exposure prophylaxis among hematologic malignancy patients (640 Online Views)

Justin C. Laracy, Judy Yan, Samantha N. Steiger, Carrie A. Tan, Nina Cohen, Elizabeth V. Robilotti, Jerome Fender, Sara Cohen, Neha Korde, Melissa Lee-Teh, Ariela Noy, Joseph H. Oved, Lindsey E. Roeker, Gunjan Shah, N. Esther Babady, Mini Kamboj, Susan K. Seo

https://doi.org/10.3324/haematol.2023.283015

Effect of age and treatment on predictive value of measurable residual disease: implications for clinical management of adult patients with acute myeloid leukemia (331 Online Views)

Francesco Mannelli, Matteo Piccini, Sara Bencini, Giacomo Gianfaldoni, Benedetta Peruzzi, Roberto Caporale, Barbara Scappini, Laura Fasano, Elisa Quinti, Gaia Ciolli, Andrea Pasquini, Francesca Crupi, Sofia Pilerci, Fabiana Pancani, Leonardo Signori, Danilo Tarantino, Chiara Maccari, Vivian Paradiso, Francesco Annunziato, Paola Guglielmelli, Alessandro M. Vannucchi

https://doi.org/10.3324/haematol.2023.283196

Letters to the Editor

Efficacy and toxicity of midostaurin with idarubicin and cytarabine induction in FLT3-mutated acute myeloid leukemia (282 Online Views)

Julia S. Lee, Charlotte B. Wagner, Stacy Prelewicz, Heena P. Kurish, Robert Walchack, Danielle A. Cenin, Seema Patel, Mimi Lo, Danielle Schlafer, Belinda K.T. Li, R. Donald Harvey III, Bestis Wasef, Jian Ying, Tibor Kovacsovics

https://doi.org/10.3324/haematol.2022.281967

Latexin deletion protects against radiation-induced hematopoietic damages via selective activation of Bcl-2 prosurvival pathway (192 Online Views)

Cuiping Zhang, Xiaojing Cui, Yi Liu, Fang Wang, Robert Signer, Kapana Nattamai, Daohong Zhou, Yi Zheng, Hartmut Geiger, Fengyi Wan, Ying Liang

https://doi.org/10.3324/haematol.2022.282028

CAR-T cell therapy for central nervous system lymphomas: blood and cerebrospinal fluid biology, and outcomes (341 Online Views)

Claire Lacan, Jonathan Caron, Nadine Tarantino, Baptiste Fouquet, Mustapha Cherai, Christophe Parizot, Véronique Morel, Laetitia Souchet, Madalina Uzunov, Guy Gorochov, Stéphanie Nguyen-Quoc, Elise Sourdeau, Vincent Vieillard, Makoto Miyara, Angélique Vinit, Silvia Solorzano, Carole Soussain, Caroline Houillier, Carole Metz, Brigitte Autran, Elena Litvinova, Magali Le Garff-Tavernier, Françoise Norol, Damien Roos-Weil, Sylvan Choquet, Amélie Guihot, Marine Baron

https://doi.org/10.3324/haematol.2023.282875

Exclusion of persistent mutations in splicing factor genes and isocitrate dehydrogenase 2 improves the prognostic power of molecular measurable residual disease assessment in acute myeloid leukemia (283 Online Views)

Tracy Murphy, Jinfeng Zou, Andrea Arruda, Ting Ting Wang, Zhen Zhao, Yangqiao Zheng, Vikas Gupta, Dawn Maze, Caroline McNamara, Mark D. Minden, Aaron Schimmer, Hassan Sibai, Karen Yee, Jose-Mario Capo-Chichi, Tracy Stockley, Andre Schuh, Scott V. Bratman, Steven M. Chan

https://doi.org/10.3324/haematol.2023.283510

Jun 15, 2023

Editorials
Article

Effect of two additional doses of intrathecal methotrexate during induction therapy on serious infectious toxicity in pediatric patients with acute lymphoblastic leukemia (432 Online Views)

Janina Heilmann, Simon Vieth, Anja Möricke, Andishe Attarbaschi, Draga Barbaric, Nicole Bodmer, Antonella Colombini, Luciano Dalla-Pozza, Sarah Elitzur, Shai Izraeli, Georg Mann, Felix Niggli, Daniela Silvestri, Jan Stary, Carmelo Rizzari, Maria Grazia Valsecchi, Ester Zapotocka, Martin Zimmermann, Gunnar Cario, Martin Schrappe, Valentino Conter

https://doi.org/10.3324/haematol.2022.281788

Editorials
Article

Clinical and molecular correlates of somatic and germline DDX41 variants in patients and families with myeloid neoplasms (843 Online Views)

Talha Badar, Ahmad Nanaa, James M. Foran, David Viswanatha, Aref Al-Kali, Terra Lasho, Christy Finke, Hassan B Alkhateeb, Rong He, Naseema Gangat, Mithun Shah, Ayalew Tefferi, Abhishek A Mangaonkar, Mark R Litzow, Laura J. Ongie, Timothy Chlon, Alejandro Ferrer, Mrinal M. Patnaik

https://doi.org/10.3324/haematol.2023.282867

Editorials

Articles

Salvage radiotherapy in relapsed/refractory large B-cell lymphoma after failure of CAR Tcell therapy (603 Online Views)

Hazim S. Ababneh, Andrea K. Ng, Matthew J. Frigault, Jeremy S Abramson, Patrick Connor Johnson, Caron A. Jacobson, Chirayu G. Patel

https://doi.org/10.3324/haematol.2023.282804

Characterization of genetic variants in the EGLN1/PHD2 gene identified in a European collection of patients with erythrocytosis (183 Online Views)

Marine Delamare, Amandine Le Roy, Mathilde Pacault, Loïc Schmitt, Céline Garrec, Nada Maaziz, Matti Myllykoski, Antoine Rimbert, Valéna Karaghiannis, Bernard Aral, Mark Catherwood, Fabrice Airaud, Lamisse Mansour-Hendili, David Hoogewijs, Edoardo Peroni, Salam Idriss, Valentine Lesieur, Amandine Caillaud, Karim Si-Tayeb, Caroline Chariau, Anne Gaignerie, Minke Rab, Torsten Haferlach, Manja Meggendorfer, Stéphane Bézieau, Andrea Benetti, Nicole Casadevall, Pierre Hirsch, Christian Rose, Mathieu Wemeau, Frédéric Galacteros, Bruno Cassinat, Beatriz Bellosillo, Celeste Bento, Richard van Wijk, Petro E. Petrides, Maria Luigia Randi, Mary Frances McMullin, Peppi Koivunen, François Girodon, Betty Gardie; ECYT-3 consortium (Collaborative Group)

https://doi.org/10.3324/haematol.2023.282913

Consolidative radiotherapy for residual FDG activity on day +30 post CAR T-cell therapy in non-Hodgkin lymphoma (909 Online Views)

Omran Saifi, William G Breen, Scott C Lester, William G Rule, Bradley J Stish, Allison Rosenthal, Javier Munoz, Yi Lin, Radhika Bansal, Matthew A Hathcock, Patrick B Johnston, Stephen M Ansell, Jonas Paludo, Arushi Khurana, Jose C Villasboas, Yucai Wang, Madiha Iqbal, Muhamad Alhaj Moustafa, Hemant S Murthy, Mohamed A. Kharfan-Dabaja, Jennifer L Peterson, Bradford S Hoppe

https://doi.org/10.3324/haematol.2023.283311

Aberrant MNX1 expression associated with t(7;12)(q36;p13) pediatric acute myeloid leukemia induces the disease through altering histone methylation (535 Online Views)

Ahmed Waraky, Anders Östlund, Tina Nilsson, Dieter Weichenhan, Pavlo Lutsik, Marion Bähr, Joschka Hey, Gürcan Tunali, Jenni Adamsson, Susanna Jacobsson, Mohammad Hamdy Abdelrazak Morsy, Susann Li, Linda Fogelstrand, Christoph Plass, Lars Palmqvist

https://doi.org/10.3324/haematol.2022.282255

Letters to the Editor

Hematological abnormalities in Jacobsen syndrome: Cytopenia of varying severities and morphological abnormalities in peripheral blood and bone marrow (290 Online Views)

Daiki Yamashita, Hideki Muramatsu, Atsushi Narita, Manabu Wakamatsu, Yusuke Tsumura, Daichi Sajiki, Ryo Maemura, Ayako Yamamori, Masayuki Imaya, Kotaro Narita, Shinsuke Kataoka, Rieko Taniguchi, Nobuhiro Nishio, Yusuke Okuno, Naoto Fujita, Katsuyoshi Koh, Katsutsugu Umeda, Eiji Morihana, Hideto Iwafuchi, Masafumi Ito, Seiji Kojima, Asahito Hama, Yoshiyuki Takahashi

https://doi.org/10.3324/haematol.2022.282513

Specific blood monocyte distribution in histiocytoses correlates with vascular involvement and disease activity (270 Online Views)

Jerome Razanamahery, Maxime Samson, Julien Guy, Jessica Racine, Celine Row, Hélène Greigert, Barbara Nicolas, Stephanie Francois, Jean-François Emile, Fleur Cohen-Aubart, Sylvain Audia, Julien Haroche, Bernard Bonnotte

https://doi.org/10.3324/haematol.2023.282739

Mechanisms of endothelial injury and transplant-associated thrombotic microangiopathy in tandem autologous hematopoietic stem cell transplant for neuroblastoma (285 Online Views)

Anthony Sabulski, Sheyar Abdullah, Nathan Luebbering, Benjamin Aunins, Caitlin Castillo, Kelly Lake, Alexandra Duell, Lauren Strecker, Lucille Langenberg, William Broomhead, Scott DiMeo, Elizabeth A. Odegard, Jason T. Blackard, Assem G. Ziady, Alix E. Seif, Christopher E. Dandoy, Benjamin L. Laskin, Sonata Jodele, Stella M. Davies

https://doi.org/10.3324/haematol.2023.283351

Jun 8, 2023

Editorials
Article

Gene therapy restores the transcriptional program of hematopoietic stem cells in Fanconi anemia (1038 Online Views)

Miren Lasaga, Paula Río, Amaia Vilas-Zornoza, Nuria Planell, Susana Navarro, Diego Alignani, Beatriz Fernández-Varas, Daniel Mouzo, Josune Zubicaray, Roser M. Pujol, Eileen Nicoletti, Jonathan D. Schwartz, Julián Sevilla, Marina Ainciburi, Asier Ullate-Agote, Jordi Surrallés, Rosario Perona, Leandro Sastre, Felipe Prosper, David Gomez-Cabrero, Juan A. Bueren

https://doi.org/10.3324/haematol.2022.282418

Editorials

Editorials
Case Report

One gene, two opposite phenotypes: a case report of hereditary anemia due to a loss-of-function variant in the EPAS1 gene (389 Online Views)

Barbara Eleni Rosato, Roberta Marra, Federica Del Giudice, Antonella Nostroso, Simona Gobbi, Barbara Bruschi, Paola Coccia, Vittoria Monaco, Maria Monti, Achille Iolascon, Immacolata Andolfo, Roberta Russo

https://doi.org/10.3324/haematol.2022.282457

Jun 1, 2023

Review Articles

Articles

Intestinal IgA positive plasma cells are highly sensitive indicators of alloreaction early after allogeneic transplantation and associate with both, graft-versus-host disease and relapse related mortality (458 Online Views)

Lucia Scheidler, Katrin Hippe, Sakhila Ghimire, Daniela Weber, Markus Weber, Elisabeth Meedt, Petra Hoffmann, Petra Lehn, Ralph Burkhardt, Andreas Mamilos, Matthias Edinger, Daniel Wolff, Hendrik Poeck, Matthias Evert, Andre Gessner, Wolfgang Herr, Ernst Holler

https://doi.org/10.3324/haematol.2022.282188

Azacitidine, lenalidomide and donor lymphocyte infusions for relapse of myelodysplastic syndrome, acute myeloid leukemia and chronic myelomonocytic leukemia after allogeneic transplant: the Azalena-Trial (936 Online Views)

Thomas Schroeder, Matthias Stelljes, Maximilian Christopeit, Eva Esseling, Christoph Scheid, Jan-Henrik Mikesch, Christina Rautenberg, Paul Jäger, Ron-Patrick Cadeddu, Nadja Drusenheimer, Udo Holtick, Stefan Klein, Rudolf Trenschel, Rainer Haas, Ulrich Germing, Nicolaus Kröger, Guido Kobbe

https://doi.org/10.3324/haematol.2022.282570

Increased retention of functional mitochondria in mature sickle red blood cells is associated with increased sickling tendency, hemolysis and oxidative stress. (401 Online Views)

Sofia Esperti, Elie Nader, Antoine Stier, Camille Boisson, Romain Carin, Muriel Marano, Mélanie Robert, Marie Martin, Françoise Horand, Agnes Cibiel, Céline Renoux, Robin Van Bruggen, Colin Blans, Yesim Dargaud, Philippe Joly, Alexandra Gauthier, Solène Poutrel, Marc Romana, Damien Roussel, Philippe Connes

https://doi.org/10.3324/haematol.2023.282684

Conditional survival and standardized mortality ratios of patients with severe aplastic anemia surviving at least one year after hematopoietic cell transplantation or immunosuppressive therapy (721 Online Views)

Ryotaro Nakamura, Bhavisha A. Patel, Soyoung Kim, F. Lennie Wong, Saro H. Armenian, Emma M. Groarke, Daniel A. Kessler, Kyle M. Hebert, Michael Heim, Mary Eapen, Neal S. Young

https://doi.org/10.3324/haematol.2023.282781

Characterization and clinical impact of the tumor microenvironment in post-transplant aggressive B-cell lymphomas (366 Online Views)

Suvi-Katri Leivonen, Terhi Friman, Matias Autio, Samuli Vaittinen, Andreas Wind Jensen, Francesco d’Amore, Stephen Jacques Hamilton-Dutoit, Harald Holte, Klaus Beiske, Panu E. Kovanen, Riikka Räty, Sirpa Leppä

https://doi.org/10.3324/haematol.2023.282831

Letters to the Editor

Prognostic value of early PET in patients with large B-cell lymphoma treated with anti-CD19 CAR T-cell therapy (419 Online Views)

Jennifer L. Crombie, Caron A. Jacobson, Robert Redd, Geoffrey Shouse, Alex F. Herrera, Victor A. Chow, Jordan Gauthier, Erin Mullane, Kirk Cahill, Justin Kline, Jason Romancik, Jonathon B. Cohen, Anna Saucier, Roch Houot, Philippe Armand, Brian Hess

https://doi.org/10.3324/haematol.2022.282345

Clinical outcomes of patients with myelofibrosis after immediate transition to momelotinib from ruxolitinib (1109 Online Views)

Ruben Mesa, Srdan Verstovsek, Uwe Platzbecker, Vikas Gupta, David Lavie, Pilar Giraldo, Christian Recher, Jean-Jacques Kiladjian, Stephen T. Oh, Aaron T. Gerds, Timothy Devos, Francesco Passamonti, Alessandro M. Vannucchi, Miklos Egyed, Ewa Lech-Maranda, Andrzej Pluta, Lars Nilsson, Kazuya Shimoda, Donal McLornan, Jun Kawashima, Barbara Klencke, Mei Huang, Bryan Strouse, Claire Harrison

https://doi.org/10.3324/haematol.2023.283106

May 25, 2023

Review Articles

Articles

Subgroup-specific gene expression profiles and mixed epistasis in chronic lymphocytic leukemia (476 Online Views)

Almut Lütge, Junyan Lu, Jennifer Hüllein, Tatjana Walther, Leopold Sellner, Bian Wu, Richard Rosenquist, Christopher C. Oakes, Sascha Dietrich, Wolfgang Huber, Thorsten Zenz

https://doi.org/10.3324/haematol.2022.281869

Early splenectomy in a large cohort of children with sickle cell anemia: risks and consequences (290 Online Views)

Aimen Mechraoui, Ghislaine Ithier, Justine Pages, Zinedine Haouari, Liza Ali, Arnaud Bonnard, Malika Benkerrou, Florence Missud, Berengère Koehl, Laurent Holvoet, Enora Le Roux, Valentine Brousse

https://doi.org/10.3324/haematol.2022.282556

Patient-reported treatment response in chronic graft-versus-host disease (401 Online Views)

Annie Im, Iskra Pusic, Lynn Onstad, Carrie L. Kitko, Betty K. Hamilton, Amin M. Alousi, Mary E. Flowers, Stefanie Sarantopoulos, Paul Carpenter, Jennifer White, Sally Arai, Najla El Jurdi, George Chen, Corey Cutler, Stephanie Lee, Joseph Pidala

https://doi.org/10.3324/haematol.2023.282734

Letters to the Editor

Clinical and molecular features of CBL-mutated juvenile myelomonocytic leukemia (357 Online Views)

Taro Yoshida, Hideki Muramatsu, Manabu Wakamatsu, Daichi Sajiki, Norihiro Murakami, Hironobu Kitazawa, Yasuhiro Okamoto, Rieko Taniguchi, Shinsuke Kataoka, Atsushi Narita, Asahito Hama, Yusuke Okuno, Yoshiyuki Takahashi

https://doi.org/10.3324/haematol.2022.282385

TRES, a validated three-factor comorbidity score, is associated with survival in older patients with mantle cell lymphoma (329 Online Views)

Max J. Gordon, David A. Bond, Adam S. Kittai, Neda Amirmokhtari, Abigail Steinbrunner, Allison Huffman, Victor Orellana-Noia, Geoffrey Shouse, Jonathon B. Cohen, Tycel Phillips, Alexey V. Danilov

https://doi.org/10.3324/haematol.2023.283074

May 18, 2023

Articles

Adenosine signaling inhibits erythropoiesis and promotes myeloid differentiation (463 Online Views)

Mahmoud Mikdar, Marion Serra, Elia Colin, Romain Duval, Emilie-Fleur Gauthier, Yann Lamarre, Yves Colin, Caroline Le Van Kim, Thierry Peyrard, Bérengère Koehl, Slim Azouzi

https://doi.org/10.3324/haematol.2022.281823

Outcomes after intensive chemotherapy for secondary and myeloidrelated changes acute myeloid leukemia patients aged 60 to 75 years old: a retrospective analysis from the PETHEMA registry (461 Online Views)

David Martínez-Cuadrón, Juan E. Megías-Vericat, Cristina Gil, Teresa Bernal, Mar Tormo, Pilar Martínez-Sánchez, Carlos Rodríguez-Medina, Josefina Serrano, Pilar Herrera, José A. Pérez Simón, María J. Sayas, Juan Bergua, Esperanza Lavilla-Rubira, Maria Luz Amigo, Celina Benavente, Jose L. López Lorenzo, Manuel M. Pérez-Encinas, María B. Vidriales, Mercedes Colorado, Beatriz de Rueda, Raimundo García-Boyero, Sandra Marini, Julio García-Suárez, María López-Pavía, Maria I. Gómez-Roncero, Víctor Noriega, Aurelio López, Jorge Labrador, Ana Cabello, Claudia Sossa, Lorenzo Algarra, Mariana Stevenazzi, Antonio Solana-Altabella, Blanca Boluda, Pau Montesinos

https://doi.org/10.3324/haematol.2022.282506

Clinical and molecular correlates of somatic and germline DDX41 variants in patients and families with myeloid neoplasms (843 Online Views)

Talha Badar, Ahmad Nanaa, James M. Foran, David Viswanatha, Aref Al-Kali, Terra Lasho, Christy Finke, Hassan B Alkhateeb, Rong He, Naseema Gangat, Mithun Shah, Ayalew Tefferi, Abhishek A Mangaonkar, Mark R Litzow, Laura J. Ongie, Timothy Chlon, Alejandro Ferrer, Mrinal M. Patnaik

https://doi.org/10.3324/haematol.2023.282867

Current use of androgens in bone marrow failure disorders: a report from the Severe Aplastic Anemia Working Party of the European Society of Blood and Marrow Transplantation (979 Online Views)

Simona Pagliuca, Austin G. Kulasekararaj, Dirk-Jan Eikema, Brian Piepenbroek, Raheel Iftikhar, Tariq Mahmood Satti, Morag Griffin, Marica Laurino, Alphan Kupesiz, Yves Bertrand, Bruno Fattizzo, Ibrahim Yakoub-Agha, Mahmoud Aljurf, Paola Corti, Erika Massaccesi, Bruno Lioure, Marisa Calabuig, Matthias Klammer, Emel Unal, Depei Wu, Patrice Chevallier, Edouard Forcade, John A. Snowden, Hakan Ozdogu, Antonio Risitano, Régis Peffault de Latour

https://doi.org/10.3324/haematol.2023.282935

Impact of viral hepatitis therapy in multiple myeloma and other monoclonal gammopathies linked to hepatitis B or C viruses (483 Online Views)

Alba Rodríguez-García, Nicolas Mennesson, Gema Hernandez-Ibarburu, María Luz Morales, Laurent Garderet, Lorine Bouchereau, Sophie Allain-Maillet, Eric Piver, Irene Marbán, David Rubio, Edith Bigot-Corbel, Joaquín Martínez-López, María Linares, Sylvie Hermouet

https://doi.org/10.3324/haematol.2023.283096

Letters to the Editor

Comments

May 11, 2023

Editorials

Articles

Aging-induced pseudouridine synthase 10 impairs hematopoietic stem cells (513 Online Views)

Yuqian Wang, Zhenzhen Zhang, Hanqing He, Jinghui Song, Yang Cui, Yunan Chen, Yuan Zhuang, Xiaoting Zhang, Mo Li, Xinxiang Zhang, Michael Q. Zhang, Minglei Shi, Chengqi Yi, Jianwei Wang

https://doi.org/10.3324/haematol.2022.282211

Ferroportin inhibitor vamifeport ameliorates ineffective erythropoiesis in a mouse model of β-thalassemia with blood transfusions (366 Online Views)

Natarajaswamy Kalleda, Anna Flace, Patrick Altermatt, Giada Ingoglia, Cédric Doucerain, Naja Nyffenegger, Franz Dürrenberger, Vania Manolova

https://doi.org/10.3324/haematol.2022.282328

Safety and efficacy of zinpentraxin alfa as monotherapy or in combination with ruxolitinib in myelofibrosis: stage I of a phase II trial (828 Online Views)

Srdan Verstovsek, Lynda Foltz, Vikas Gupta, Robert Hasserjian, Taghi Manshouri, John Mascarenhas, Ruben Mesa, Olga Pozdnyakova, Ellen Ritchie, Ivo Veletic, Katia Gamel, Habib Hamidi, Lyrialle Han, Brian Higgins, Kerstin Trunzer, Marianne Uguen, Dao Wang, Tarec Christoffer El-Galaly, Boyan Todorov, Jason Gotlib

https://doi.org/10.3324/haematol.2022.282411

Letters to the Editor

KIR3DL2 may represent a novel therapeutic target in aggressive systemic peripheral T-cell lymphoma (426 Online Views)

Amandine Decroos, Morgane Cheminant, Julie Bruneau, Sylvain Carras, Vincent Parinet, Laura Pelletier, Laetitia Lacroix, Nadine Martin, Jérôme Giustiniani, Ludovic Lhermitte, Vahid Asnafi, Maxime Battistella, François Lemonnier, Laurence de Leval, Hélène Sicard, Cécile Bonnafous, Laurent Gauthier, Laurent Genestier, Stefano Caruso, Philippe Gaulard, Olivier Hermine, Nicolas Ortonne

https://doi.org/10.3324/haematol.2022.282220

A proposed predictive mathematical model for efficient T cell collection by leukapheresis for manufacturing chimeric antigen receptor T cells (242 Online Views)

Xinxin Huang, Gina Pei Ling Gan, Esther Hian Li Chan, Kee Khiang Heng, Susila Perumal, Rohani Salleh, Jessica Mei Ling Teo, Gaoge Xie, Jing Jing Lee, Aloysius Yew Leng Ho, William Ying Khee Hwang, Yeh Ching Linn, Yunxin Chen, Jeffrey Kim Siang Quek, Hein Than, Chandramouli Nagarajan, Francesca Lorraine Wei Inng Lim

https://doi.org/10.3324/haematol.2022.282350

Transcriptomic profiling does not refine mastocytosis diagnosis (282 Online Views)

Lars Buschhorn, Dorett I. Odoni, Johanna Geuder, Timo O. Odinius, Celina V. Wagner, Stefanie Jilg, Ulrike Höckendorf, Adam Wahida, Matthias Schlesner, Andreas Reiter, Mohamad Jawhar, Philipp J. Jost

https://doi.org/10.3324/haematol.2022.282617

May 4, 2023

Articles

B-cell receptor reactivity against Rothia mucilaginosa in nodular lymphocyte-predominant Hodgkin lymphoma (538 Online Views)

Lorenz Thurner, Natalie Fadle, Evi Regitz, Sophie Roth, Onur Cetin, Igor Age Kos, Simon Mauro Hess, Julia Bein, Rainer Maria Bohle, Martine Vornanen, Christer Sundström, Laurence de Leval, Enrico Tiacci, Peter Borchmann, Andreas Engert, Viola Poeschel, Gerhard Held, Eva C. Schwarz, Frank Neumann, Klaus-Dieter Preuss, Markus Hoth, Ralf Küppers, Karola Lehman, Martin-Leo Hansmann, Sören L. Becker, Moritz Bewarder, Sylvia Hartmann

https://doi.org/10.3324/haematol.2023.282698

Letters to the Editor

Apr 27, 2023

Articles

Platelet phosphatidylserine is the critical mediator of thrombosis in heparin-induced thrombocytopenia (513 Online Views)

Jan Zlamal, Anurag Singh, Karoline Weich, Hisham Jaffal, Günalp Uzun, Lisann Pelzl, Karina Althaus, Tamam Bakchoul

https://doi.org/10.3324/haematol.2022.282275

miRInactivation of p53 provides a competitive advantage to del(5q) myelodysplastic syndrome hematopoietic stem cells during inflammation (1091 Online Views)

Tomoya Muto, Callum S. Walker, Puneet Agarwal, Eric Vick, Avery Sampson, Kwangmin Choi, Madeline Niederkorn, Chiharu Ishikawa, Kathleen Hueneman, Melinda Varney, Daniel T. Starczynowski

https://doi.org/10.3324/haematol.2022.282349

Randomized phase II study of weekly carfilzomib 70 mg/m2 and dexamethasone with or without cyclophosphamide in relapsed and/or refractory multiple myeloma patients (1114 Online Views)

Borja Puertas, Verónica González-Calle, Anna Sureda, María José Moreno, Albert Oriol, Esther González, Laura Rosiñol, Jordi López, Fernando Escalante, Joaquín Martínez-Lopez, Estrella Carrillo, Esther Clavero, Rafael Ríos-Tamayo, Beatriz Rey-Bua, Ana Pilar González-Rodríguez, Victoria Dourdil, Felipe de Arriba, Sonia González, Jaime Pérez-de-Oteyza, Miguel T. Hernández, Aránzazu García-Mateo, Joan Bargay, Joan Bladé, Juan José Lahuerta, Jesús F. San Miguel, Enrique M. Ocio, María-Victoria Mateos

https://doi.org/10.3324/haematol.2022.282490

Effect of cumulative dose of brentuximab vedotin maintenance in relapsed/refractory classical Hodgkin lymphoma after autologous stem cell transplant: an analysis of real-world outcomes (808 Online Views)

Charlotte B. Wagner, Ken Boucher, Adrienne Nedved, Ivana N. Micallef, Sanjal Desai, Haris Hatic, Gaurav Goyal, Erin Zacholski, Amanda Fegley, Audrey M. Sigmund, David A. Bond, Courtney Samuels, Manali K. Kamdar, Sheeba Ba Aqeel, Pallawi Torka, Kira MacDougall, Azra Borogovac, Sridevi Rajeeve, Suchitra Sundaram, Kalub Fedak, Dipenkumar Modi, Elizabeth Travers, Sabarish Ayyappan, Nitin Chilakamarri, Elizabeth A. Brem, Daniel A. Ermann, Lindsey A. Fitzgerald, Boyu Hu, Deborah M. Stephens, Harsh Shah

https://doi.org/10.3324/haematol.2023.282780

Letters to the Editor

Menin inhibitor ziftomenib (KO-539) synergizes with drugs targeting chromatin regulation or apoptosis and sensitizes acute myeloid leukemia with MLL rearrangement or NPM1 mutation to venetoclax (937 Online Views)

Johanna Rausch, Margarita M. Dzama, Nadezda Dolgikh, Hanna L. Stiller, Stephan R. Bohl, Catharina Lahrmann, Kerstin Kunz, Linda Kessler, Hakim Echchannaoui, Chun-Wei Chen, Thomas Kindler, Konstanze Döhner, Francis Burrows, Matthias Theobald, Daniel Sasca, Michael W.M. Kühn

https://doi.org/10.3324/haematol.2022.282160

TET2 mutational status affects myelodysplastic syndrome evolution to chronic myelomonocytic leukemia (477 Online Views)

Violaine Tran Quang, Benjamin Podvin, Christophe Desterke, Sihem Tarfi, Quentin Barathon, Bouchra Badaoui, Nicolas Freynet, Vincent Parinet, Mathieu Leclerc, Sébastien Maury, Eric Solary, Dorothée Selimoglu-Buet, Nicolas Duployez, Orianne Wagner-Ballon, Ivan Sloma

https://doi.org/10.3324/haematol.2022.282528

Case Reports

One gene, two opposite phenotypes: a case report of hereditary anemia due to a loss-of-function variant in the EPAS1 gene (389 Online Views)

Barbara Eleni Rosato, Roberta Marra, Federica Del Giudice, Antonella Nostroso, Simona Gobbi, Barbara Bruschi, Paola Coccia, Vittoria Monaco, Maria Monti, Achille Iolascon, Immacolata Andolfo, Roberta Russo

https://doi.org/10.3324/haematol.2022.282457

Novel FIP1L1::KIT fusion in a myeloid neoplasm with eosinophilia, T-lymphoblastic transformation, and dasatinib response (315 Online Views)

Aseel Alsouqi, Jeffrey Kleinberger, Taylor S Werner, Rashid Awan, Saurav Chopra, Bryan Rea, Nidhi Aggarwal, Svetlana A. Yatsenko, Rafic Farah, Nathanael G. Bailey

https://doi.org/10.3324/haematol.2022.282636

Spotlight Review

Apr 20, 2023

Articles

Real-world study of the efficacy and safety of belantamab mafodotin (GSK2857916) in relapsed or refractory multiple myeloma based on data from the nominative ATU in France: the IFM 2020-04 study (993 Online Views)

Alexis Talbot, Arthur Bobin, Léa Tabone, Jérôme Lambert, Catherine Boccaccio, Cécile Deal, Marie-Odile Petillon, Olivier Allangba, Philippe Agape, Pierre Arnautou, Rakiba Belkhir, Sylvie Cailleres, Driss Chaoui, Marie-Lorraine Chrétien, Olivier Decaux, Samantha Schulmann, Laurent Frenzel, Lauris Gastaud, Antoine Huart, Cyrille Hulin, Lionel Karlin, Kamel Laribi, Ronan Le Calloch, Pascal Lenain, Margaret Macro, Salomon Manier, Lydia Montes, Stéphane Moreau, Philippe Moreau, Véronique Morel, James Norwood, Frédérique Orsini Piocelle, Aurore Perrot, Gian Matteo Pica, Philippe Rey, Anna Schmitt, Anne-Marie Stoppa, Mourad Tiab, Cyrille Touzeau, Valérie Vidal, Marguerite Vignon, Laure Vincent, Zoé Van De Wyngaert, Charles Zarnitsky, Naima Kerbouche, Prani Paka, Xavier Leleu, Bertrand Arnulf, Hervé Avet-Loiseau; IFM: Intergroupe Francophone du Myélome (Collaborative Group)

https://doi.org/10.3324/haematol.2022.281772

Co-targeting BCL-XL and BCL-2 by PROTAC 753B eliminates leukemia cells and enhances efficacy of chemotherapy by targeting senescent cells (1750 Online Views)

Yannan Jia, Lina Han, Cassandra L. Ramage, Zhe Wang, Connie C. Weng, Lei Yang, Simona Colla, Helen Ma, Weiguo Zhang, Michael Andreeff, Naval Daver, Nitin Jain, Naveen Pemmaraju, Kapil Bhalla, Satu Mustjoki, Peiyi Zhang, Guangrong Zheng, Daohong Zhou, Qi Zhang, Marina Konopleva

https://doi.org/10.3324/haematol.2022.281915

Reticulocytes in donor blood units enhance red blood cell alloimmunization (554 Online Views)

Tiffany A. Thomas, Annie Qiu, Christopher Y. Kim, Dominique E. Gordy, Anabel Miller, Maria Tredicine, Monika Dzieciatkowska, Flavia Dei Zotti, Eldad A. Hod, Angelo D’Alessandro, James C. Zimring, Steven L. Spitalnik, Krystalyn E. Hudson

https://doi.org/10.3324/haematol.2023.282815

Apr 13, 2023

Articles

Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis (1006 Online Views)

Chatphatai Moonla, Chantana Polprasert, Patcharee Komvilaisak, Thanawat Rattanathammethee, Sunisa Kongkiatkamon, Kitsada Wudhikarn, Sirorat Kobbuaklee, Pitchayut Boonyabaramee, Nuanrat Tangcheewinsirikul, Samart Pakakasama, Piya Rujkijyanont, Chane Choed-Amphai, Kamon Phuakpet, Saranya Pongudom, Udomsak Bunworasate, Narittee Sukswai, Darintr Sosothikul, Ponlapat Rojnuckarin

https://doi.org/10.3324/haematol.2022.282419

Adolescents and young adults with newly diagnosed primary immune thrombocytopenia (651 Online Views)

Alexandra Schifferli, Guillaume Moulis, Bertrand Godeau, Thierry Leblanc, Nathalie Aladjidi, Marc Michel, Guy Leverger, Mohsen Elalfy, John Grainger, Meera Chitlur, Andrea Heiri, Susanne Holzhauer, Gautier le Gavrian, Paul Imbach, Thomas Kühne

https://doi.org/10.3324/haematol.2022.282524

Higher-dose venetoclax with measurable residual diseaseguided azacitidine discontinuation in newly diagnosed acute myeloid leukemia (931 Online Views)

Jonathan A. Gutman, Amanda Winters, Andrew Kent, Maria Amaya, Christine McMahon, Clayton Smith, Craig T. Jordan, Brett Stevens, Mohammad Minhajuddin, Shanshan Pei, Jeffrey Schowinsky, Jennifer Tobin, Kelly O’Brien, Angela Falco, Elizabeth Taylor, Constance Brecl, Katie Zhou, Phuong Ho, Connor Sohalski, Jessica Dell-Martin, Olivia Ondracek, Diana Abbott, Daniel A. Pollyea

https://doi.org/10.3324/haematol.2023.282681

Letters to the Editor

Characterization of a novel MEF2D-BCL9 fusion-positive acute lymphoblastic leukemia cell line (389 Online Views)

Inge van Outersterp, Femke M. Hormann, Alex Q. Hoogkamer, Aurélie Boeree, Stijn A. van den Broek, Monique L. den Boer, Judith M. Boer

https://doi.org/10.3324/haematol.2022.281712

Case Reports

Apr 6, 2023

Editorials
Letter to the Editor

B-lineage acute lymphoblastic leukemia causes cell autonomous defects in long-term hematopoietic stem cell function. (645 Online Views)

Christina T. Jensen, Josefine Åhsberg, Johanna Tingvall-Gustafsson, Rajesh Somasundaram, Stefan Lang, Jonas Ungerbäck, Anna Porwit, Shamit Soneji, Mikael Sigvardsson

https://doi.org/10.3324/haematol.2022.282430

Articles

Effect of two additional doses of intrathecal methotrexate during induction therapy on serious infectious toxicity in pediatric patients with acute lymphoblastic leukemia (432 Online Views)

Janina Heilmann, Simon Vieth, Anja Möricke, Andishe Attarbaschi, Draga Barbaric, Nicole Bodmer, Antonella Colombini, Luciano Dalla-Pozza, Sarah Elitzur, Shai Izraeli, Georg Mann, Felix Niggli, Daniela Silvestri, Jan Stary, Carmelo Rizzari, Maria Grazia Valsecchi, Ester Zapotocka, Martin Zimmermann, Gunnar Cario, Martin Schrappe, Valentino Conter

https://doi.org/10.3324/haematol.2022.281788

Gene therapy restores the transcriptional program of hematopoietic stem cells in Fanconi anemia (1038 Online Views)

Miren Lasaga, Paula Río, Amaia Vilas-Zornoza, Nuria Planell, Susana Navarro, Diego Alignani, Beatriz Fernández-Varas, Daniel Mouzo, Josune Zubicaray, Roser M. Pujol, Eileen Nicoletti, Jonathan D. Schwartz, Julián Sevilla, Marina Ainciburi, Asier Ullate-Agote, Jordi Surrallés, Rosario Perona, Leandro Sastre, Felipe Prosper, David Gomez-Cabrero, Juan A. Bueren

https://doi.org/10.3324/haematol.2022.282418

Letters to the Editor

Clinical and laboratory diversity of diffuse large B-cell lymphomas in children with Nijmegen breakage syndrome (414 Online Views)

Agata Pastorczak, Bartosz Szmyd, Marcin Braun, Joanna Madzio, Kamila Wypyszczak, Pawel Sztromwasser, Wojciech Fendler, Marzena Wojtaszewska, Jedrzej Chrzanowski, Wieslawa Grajkowska, Hanna Gregorek, Anna Wakulinska, Bernarda Kazanowska, Zdenka Krenova, Dilys D. Weijers, Roland P. Kuiper, Wojciech Mlynarski

https://doi.org/10.3324/haematol.2022.282325

Functional, biochemical, molecular and clinical characterization of antithrombin c.1157T>C (p.Ile386Thr), a recurrent Polish variant with a founder effect (347 Online Views)

Anna Weronska, Belen de la Morena-Barrio, Sarah Goldman-Mazur, Maria Eugenia de la Morena-Barrio, José Padilla, Antonia Miñano, Pedro Garrido, Jacek Treliński, Daniel Piotr Potaczek, Anita Szczepanek, Anetta Undas, Javier Corral, Ewa Wypasek

https://doi.org/10.3324/haematol.2022.282459

Measurable residual disease-guided therapy in intermediate-risk acute myeloid leukemia patients is a valuable strategy in reducing allogeneic transplantation without negatively affecting survival (569 Online Views)

Jesse M. Tettero, Lok Lam Ngai, Costa Bachas, Dimitri A. Breems, Thomas Fischer, Bjorn T. Gjertsen, Patrycja Gradowska, Laimonas Griskevicius, Jeroen J.W.M. Janssen, Gunnar Juliusson, Johan Maertens, Markus G. Manz, Thomas Pabst, Jakob Passweg, Kimmo Porkka, Peter J.M. Valk, Bob Löwenberg, Gert J. Ossenkoppele, Jacqueline Cloos

https://doi.org/10.3324/haematol.2022.282639

Examining the impact of age on the prognostic value of ELN-2017 and ELN-2022 acute myeloid leukemia risk stratifications: a report from the SWOG Cancer Research Network (460 Online Views)

Christina M. Termini, Anna Moseley, Megan Othus, Frederick R. Appelbaum, Thomas R. Chauncey, Harry P. Erba, Min Fang, Stanley C. Lee, Jasmine Naru, Era L. Pogosova-Agadjanyan, Jerald P. Radich, Cheryl L. Willman, Feinan Wu, Soheil Meshinchi, Derek L. Stirewalt

https://doi.org/10.3324/haematol.2023.282733

Mar 30, 2023

Letters to the Editor

Subcutaneous azacitidine maintenance in transplantineligible patients with acute myeloid leukemia: a single-center retrospective study (589 Online Views)

Natacha Johnson, Marie Templé, Chloe Friedrich, Lise Willems, Rudy Birsen, Marguerite Vignon, Paul Deschamps, Patricia Franchi, Johanna Mondesir, Benedicte Deau-Fischer, Elsa Miekoutima, Ismaël Boussaid, Nicolas Chapuis, Olivier Kosmider, Didier Bouscary, Jerome Tamburini, Justine Decroocq

https://doi.org/10.3324/haematol.2022.282009

Mar 23, 2023

Articles

Letters to the Editor

Chemotherapy in solitary bone plasmacytoma to prevent evolution to multiple myeloma (360 Online Views)

Sophia Ascione, Stéphanie Harel, Florent L. Besson, Rakiba Belkhir, Julien Henry, Bruno Royer, Bertrand Arnulf, Xavier Mariette, Raphaèle Seror

https://doi.org/10.3324/haematol.2022.282214

Survival outcomes with oral azacitidine maintenance in patients with acute myeloid leukemia in remission by receipt of initial chemotherapy: subgroup analyses from the phase III QUAZAR AML-001 trial (797 Online Views)

Andrew H. Wei, Gail J. Roboz, Herve Dombret, Hartmut Dohner, Andre C. Schuh, Pau Montesinos, Dominik Selleslag, Sergey N. Bondarenko, Thomas Prebet, Yinzhi Lai, Barry Skikne, C.L. Beach, Farhad Ravandi

https://doi.org/10.3324/haematol.2022.282296

High-risk additional cytogenetic aberrations in a Dutch chronic phase chronic myeloid leukemia patient population (384 Online Views)

Camille C.B. Kockerols, Inge G.P. Geelen, Mark-David Levin, Jeroen J.W.M. Janssen, H. Berna Beveloo, Avinash G. Dinmohamed, Mels Hoogendoorn, Jan J. Cornelissen, Peter E. Westerweel

https://doi.org/10.3324/haematol.2022.282447

Risk of relapse after SARS-CoV-2 vaccine in the Milan cohort of thrombotic thrombocytopenic purpura patients (434 Online Views)

Marco Capecchi, Pasqualina De Leo, Maria Abbattista, Ilaria Mancini, Pasquale Agosti, Marina Biganzoli, Chiara Suffritti, Barbara Ferrari, Anna Lecchi, Silvia La Marca, Lidia Padovan, Erica Scalambrino, Marigrazia Clerici, Armando Tripodi, Andrea Artoni, Roberta Gualtierotti, Flora Peyvandi

https://doi.org/10.3324/haematol.2022.282478

Spotlight Review

Mar 16, 2023

Letters to the Editor

Mar 9, 2023

Editorials

Articles

Impact of central nervous system involvement in adult patients with Philadelphia-negative acute lymphoblastic leukemia: a GRAALL-2005 study (472 Online Views)

Corentin Orvain, Sylvain Chantepie, Xavier Thomas, Martine Escofrre-Barbe, Francoise Huguet, Yohan Desbrosses, Gaelle Guillerm, Madalina Uzunov, Thibaut Leguay, Sarah Barbieux, Norbert Vey, Patrice Chevallier, Jean-Valere Malfuson, Stephane Lepretre, Michael Baumann, Murat Aykut, Abdelaziz Chaib, Magalie Joris, Hacene Zerazhi, Georg Stussi, Jacques Chapiro, Celine Berthon, Caroline Bonmati, Eric Jourdan, Diana Carp, Amb roise Marcais, Maria-Pilar Gallego-Hernanz, Iona Vaida, Karin Bilger, Alban Villate, Florence Pasquier, Yves Chalandon, Sebastien Maury, Veronique Lheritier, Norbert Ifrah, Herve Dombret, Nicolas Boissel, Mathilde Hunault-Berger.

https://doi.org/10.3324/haematol.2022.282332

Letters to the Editor

Post-transplantation Burkitt lymphoma: a retrospective study of 55 patients (428 Online Views)

Pierre Walczak, Sylvain Choquet, Jacques Dantal, David Boutboul, Felipe Suarez, Marine Baron, Veronique Morel, Thomas Cluzeau, Mohamed Touati, Michelle Elias, Emmanuel Bachy, Emmanuelle Nicolas-Virelizier, Roch Houot, Geoffroy Venton, Caroline Jacquet, Marie-Pierre Moles-Moreau, Fabrice Jardin, Eric Durot, Noureddine Balegroune, Laure Ecotiere, Romain Guieze, Nassim Kamar, Loic Ysebaert, Lionel Couzi, Hugo Gonzalez, Louise Roulin, Kevin Ou, Sophie Caillard, Heiner Zimmermann, Ralf Ulrich Trappe, Damien Roos-Weil

https://doi.org/10.3324/haematol.2022.282297

The oncogenetic landscape and clinical impact of BCL11B alterations in adult and pediatric T-cell acute lymphoblastic leukemia (476 Online Views)

Marie Emilie Dourthe, Guillaume P. Andrieu, Amandine Potier, Estelle Balducci, Julie Guerder, Mathieu Simonin, Lucien Courtois, Arnaud Petit, Elizabeth Macintyre, Nicolas Boissel, André Baruchel, Vahid Asnafi

https://doi.org/10.3324/haematol.2022.282605

Mar 2, 2023

Letters to the Editor

KMT2A partner genes in infant acute lymphoblastic leukemia have prognostic significance and correlate with age, white blood cell count, sex, and central nervous system involvement: a Children’s Oncology Group P9407 trial study (505 Online Views)

Blaine W. Robinson, John A. Kairalla, Meenakshi Devidas, Andrew J. Carroll, Richard C. Harvey, Nyla A. Heerema, Cheryl L. Willman, Amanda R. Ball, Elliot C. Woods, Nancy C. Ballantyne, Karen A. Urtishak, Frederick G. Behm, Gregory H. Reaman, Joanne M. Hilden, Bruce M. Camitta, Naomi J. Winick, Jeanette Pullen, William L. Carroll, Stephen P. Hunger, ZoAnn E. Dreyer, Carolyn A. Felix

https://doi.org/10.3324/haematol.2022.281552

B-lineage acute lymphoblastic leukemia causes cell autonomous defects in long-term hematopoietic stem cell function. (645 Online Views)

Christina T. Jensen, Josefine Åhsberg, Johanna Tingvall-Gustafsson, Rajesh Somasundaram, Stefan Lang, Jonas Ungerbäck, Anna Porwit, Shamit Soneji, Mikael Sigvardsson

https://doi.org/10.3324/haematol.2022.282430

Outcome of patients with acute myeloid leukemia following failure of frontline venetoclax plus hypomethylating agent therapy (561 Online Views)

Naseema Gangat, Rimal Ilyas, Isla M Johnson, Kristen McCullough, Aref Al-Kali, Hassan B Alkhateeb, Kebede H Begna, Abhishek Mangaonkar, Mark R Litzow, William Hogan, Mithun Shah, Mrinal M Patnaik, Animesh Pardanani, Ayalew Tefferi

https://doi.org/10.3324/haematol.2022.282677

Spotlight Review

Feb 23, 2023

Letters to the Editor

Impact of vincristine dose reduction on outcomes of patients with aggressive B-cell lymphoma treated with (R)-CHOP (696 Online Views)

Moritz Bewarder, Dominic Kaddu-Mulindwa, Igor Age Kos, Vadim Lesan, Gerhard Held, Viola Poeschel, Lorenz Thurner, Joerg Thomas Bittenbring, Norbert Schmitz, Lorenz Truemper, Michael Pfreundschuh, Konstantinos Christofyllakis, Markus Loeffler, Bettina Altmann, Marita Ziepert

https://doi.org/10.3324/haematol.2022.282126

Aug 19, 2021

Errata Corrige

Long-term outcomes from the phase II L-MIND study of tafasitamab (MOR208) plus lenalidomide in patients with relapsed or refractory diffuse large B-cell lymphoma (3144 Online Views)

Johannes Duell, Kami J. Maddocks, Eva González-Barca, Wojciech Jurczak, Anna Marina Liberati, Sven de Vos, Zsolt Nagy, Aleš Obr, Gianluca Gaidano, Pau Abrisqueta, Nagesh Kalakonda, Marc André, Martin Dreyling, Tobias Menne, Olivier Tournilhac, Marinela Augustin, Andreas Rosenwald, Maren Dirnberger-Hertweck, Johannes Weirather, Sumeet Ambarkhane, Gilles Salles

https://doi.org/10.3324/haematol.2021.279802

May 10, 2018

Articles

GRP94 rewires and buffers the FLT3-ITD signaling network and promotes survival of acute myeloid leukemic stem cells (1209 Online Views)

Beibei Zhang, Pilar Ayuda Durán, Laure Piechaczyk, Yngvar Fløisand, Mireia Mayoral Safont Safont, Ida Tveit Karlsen, Zina Fandalyuk, Dagim Tadele, Pepijn van Mierlo, Alexander D. Rowe, Joseph M. Robertson, Bjørn Tore Gjertsen, Emmet McCormack, Jorrit M. Enserink, Bjørn Tore Gjertsen Group, Emmet McCormack Group

https://doi.org/10.3324/haematol.2018.189399