Open access journal of the Ferrata-Storti Foundation, a non-profit organization
Articles

Three-year safety, efficacy, and renal outcomes of mitapivat treatment in sickle cell disease: results from the phase 2 open-label study

Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht
Division of Hematology/Oncology, University of Illinois Hospital and Health Sciences System, Chicago, IL
Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands; Department of Central Diagnostic Laboratory - Research, University Medical Center Utrecht, Utrecht University, Utrecht
Department of Central Diagnostic Laboratory - Research, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands; Department of Hematology, Erasmus University Medical Center, Rotterdam
Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht
Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht
Department of Hematology, Erasmus University Medical Center, Rotterdam
Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children's Hospital University Medical Center Rotterdam, Rotterdam
Department of Hematology, Amsterdam University Medical Center, University of Amsterdam, Amsterdam
Department of Hematology, Amsterdam University Medical Center, University of Amsterdam, Amsterdam
Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht
Division of Hematology/Oncology, University of Illinois Hospital and Health Sciences System, Chicago, IL
Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht
Haematologica Early view Feb 26, 2026 https://doi.org/10.3324/haematol.2025.289105

Abstract

Not available.

Figures & Tables

Article Information

Early view : Articles
 
DOI
https://doi.org/10.3324/haematol.2025.289105
 
Published
2026-02-26
Published By
Ferrata Storti Foundation, Pavia, Italy
Print ISSN
0390-6078
Online ISSN
1592-8721
 
Creative Commons License

This work is licensed under a Creative Commons Attribution 4.0 International License.

Article Usage

Online Views
91
PDF Downloads
43

Statistics from Altmetric.com

No Data
Navigate
For Authors
For Reviewers
For Advertisers
Education
Privacy
More
Copyright © 2026 by the Ferrata Storti Foundation | Web design ￫ | Development ￫
ISSN 0390-6078 print | ISSN 1592-8721 online