Letters to the Editor

Inclusion of a shRNA targeting BCL11A into a β-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobin

Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia; Graduate Program in Basic and Applied Biology (GABBA), Institute of Biomedical Sciences Abel Salazar, University of Porto, Porto
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Cell Engineering Division, RIKEN BioResource Research Center, Tsukuba
Department of Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
Department of Pediatrics, Hematology, The Children’s Hospital of Philadelphia, Philadelphia
#SPL and DJ contributed equally as co-senior authors.
Haematologica Early view May 27, 2021 https://doi.org/10.3324/haematol.2020.276634