Perspective Articles

Next-generation strategies to improve safety and efficacy of adeno-associated virus-based gene therapy for hemophilia: lessons from clinical trials in other gene therapies

Dipartimento di Medicina Clinica e Chirurgia, Federico II University, School of Medicine, Napoli
The Haemophilia Center of the Medical Clinic, University Hospital Frankfurt/Main
Center for Bleeding Disorders and Coagulation, Department of Oncology, Careggi University Hospital, Florence
Angelo Bianchi Bonomi Haemophilia and Thrombosis Center, Fondazione Luigi Villa, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
Haematologica Early view Mar 7, 2024