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Jaako P, Debnath S, Olsson K, Modlich U, Rothe M, Schambach A, Flygare J, Karlsson S. Gene therapy cures the anemia and lethal bone marrow failure in a mouse model of RPS19-deficient Diamond-Blackfan anemia. Haematologica [Internet]. 2014Dec.3 [cited 2026Nov.2];99(12):1792-8. Available from: https://haematologica.org/article/view/7219