1.
Di Minno G, Miesbach W, Castaman G, Peyvandi F. Next-generation strategies to improve safety and efficacy of adeno-associated virus-based gene therapy for hemophilia: lessons from clinical trials in other gene therapies. haematol [Internet]. 2024Dec.1 [cited 2025Dec.15];109(12):3879-91. Available from: https://haematologica.org/article/view/haematol.2023.284622