Saultier P, Pecci A. Is hematopoietic stem cell transplantation indicated in THPO-mutated congenital amegakaryocytic thrombocytopenia? Comment on: "Avatrombopag as a novel salvage therapy for refractory thrombocytopenia in THPO-mutated congenital amegakaryocytic thrombocytopenia after allogeneic hematopoietic stem cell transplantation". Haematologica; https://doi.org/10.3324/haematol.2026.302090 [Early view].