1.
Pires Lourenco S, Jarocha D, Ghiaccio V, Guerra A, Abdulmalik O, La P, Zezulin A, Smith-Whitley K, Kwiatkowski JL, Guzikowski V, Nakamura Y, Raabe T, Breda L, Rivella S. Inclusion of a short hairpin RNA targeting <i>BCL11A</i&gt; into a β-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobin. Haematologica 2021;106(10):2740-2745; https://doi.org/10.3324/haematol.2020.276634.