Kuppens, Geoffrey Z.L., Maria Armila D. Ruiz, Myrthe J. van Dijk, Minke A.E. Rab, Cleo Derichs, Joline Saes, Anita W. Rijneveld, Marjon H. Cnossen, Erfan Nur, Bart J. Biemond, Marije Bartels, Santosh L. Saraf, and Eduard J. van Beers. 2020. “Three-Year Safety, Efficacy, and Renal Outcomes of Mitapivat Treatment in Sickle Cell Disease: Results from the Phase 2 Open-Label Study”. Haematologica, September. Pavia, Italy. https://doi.org/10.3324/haematol.2025.289105.