Di Minno, Giovanni, Wolfgang Miesbach, Giancarlo Castaman, and Flora Peyvandi. 2020. “Next-Generation Strategies to Improve Safety and Efficacy of Adeno-Associated Virus-Based Gene Therapy for Hemophilia: Lessons from Clinical Trials in Other Gene Therapies”. Haematologica, September. Pavia, Italy. https://doi.org/10.3324/haematol.2023.284622.